Gersbach CA - Search Results

1

AAV CRISPR editing rescues cardiac and muscle function for 18 months in dystrophic mice.

Hakim CH, Wasala NB, Nelson CE, Wasala LP, Yue Y, Louderman JA, Lessa TB, Dai A, Zhang K, Jenkins GJ, Nance ME, Pan X, Kodippili K, Yang NN, Chen SJ, Gersbach CA, Duan D. Hakim CH, et al. Among authors: gersbach ca. JCI Insight. 2018 Dec 6;3(23):e124297. doi: 10.1172/jci.insight.124297. JCI Insight. 2018. PMID: 30518686 Free PMC article.

2

Reading frame correction by targeted genome editing restores dystrophin expression in cells from Duchenne muscular dystrophy patients.

Ousterout DG, Perez-Pinera P, Thakore PI, Kabadi AM, Brown MT, Qin X, Fedrigo O, Mouly V, Tremblay JP, Gersbach CA. Ousterout DG, et al. Among authors: gersbach ca. Mol Ther. 2013 Sep;21(9):1718-26. doi: 10.1038/mt.2013.111. Epub 2013 Jun 4. Mol Ther. 2013. PMID: 23732986 Free PMC article.

3

Correction of dystrophin expression in cells from Duchenne muscular dystrophy patients through genomic excision of exon 51 by zinc finger nucleases.

Ousterout DG, Kabadi AM, Thakore PI, Perez-Pinera P, Brown MT, Majoros WH, Reddy TE, Gersbach CA. Ousterout DG, et al. Among authors: gersbach ca. Mol Ther. 2015 Mar;23(3):523-32. doi: 10.1038/mt.2014.234. Epub 2014 Dec 10. Mol Ther. 2015. PMID: 25492562 Free PMC article.

4

Multiplex CRISPR/Cas9-based genome editing for correction of dystrophin mutations that cause Duchenne muscular dystrophy.

Ousterout DG, Kabadi AM, Thakore PI, Majoros WH, Reddy TE, Gersbach CA. Ousterout DG, et al. Among authors: gersbach ca. Nat Commun. 2015 Feb 18;6:6244. doi: 10.1038/ncomms7244. Nat Commun. 2015. PMID: 25692716 Free PMC article.

5

Highly specific epigenome editing by CRISPR-Cas9 repressors for silencing of distal regulatory elements.

Thakore PI, D'Ippolito AM, Song L, Safi A, Shivakumar NK, Kabadi AM, Reddy TE, Crawford GE, Gersbach CA. Thakore PI, et al. Among authors: gersbach ca. Nat Methods. 2015 Dec;12(12):1143-9. doi: 10.1038/nmeth.3630. Epub 2015 Oct 26. Nat Methods. 2015. PMID: 26501517 Free PMC article.

6

In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy.

Nelson CE, Hakim CH, Ousterout DG, Thakore PI, Moreb EA, Castellanos Rivera RM, Madhavan S, Pan X, Ran FA, Yan WX, Asokan A, Zhang F, Duan D, Gersbach CA. Nelson CE, et al. Among authors: gersbach ca. Science. 2016 Jan 22;351(6271):403-7. doi: 10.1126/science.aad5143. Epub 2015 Dec 31. Science. 2016. PMID: 26721684 Free PMC article.

7

Cas9 loosens its grip on off-target sites.

Nelson CE, Gersbach CA. Nelson CE, et al. Among authors: gersbach ca. Nat Biotechnol. 2016 Mar;34(3):298-9. doi: 10.1038/nbt.3501. Nat Biotechnol. 2016. PMID: 26963555 No abstract available.

8

Engineering Delivery Vehicles for Genome Editing.

Nelson CE, Gersbach CA. Nelson CE, et al. Among authors: gersbach ca. Annu Rev Chem Biomol Eng. 2016 Jun 7;7:637-62. doi: 10.1146/annurev-chembioeng-080615-034711. Epub 2016 Apr 21. Annu Rev Chem Biomol Eng. 2016. PMID: 27146557 Review.

9

Gene therapies that restore dystrophin expression for the treatment of Duchenne muscular dystrophy.

Robinson-Hamm JN, Gersbach CA. Robinson-Hamm JN, et al. Among authors: gersbach ca. Hum Genet. 2016 Sep;135(9):1029-40. doi: 10.1007/s00439-016-1725-z. Epub 2016 Aug 20. Hum Genet. 2016. PMID: 27542949 Free PMC article. Review.

10

Genetic engineering: Chemical control for CRISPR editing.

Hilton IB, Gersbach CA. Hilton IB, et al. Among authors: gersbach ca. Nat Chem Biol. 2017 Jan;13(1):2-3. doi: 10.1038/nchembio.2243. Epub 2016 Nov 7. Nat Chem Biol. 2017. PMID: 27820804 No abstract available.

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