Focal lesions following intracerebral gene therapy for mucopolysaccharidosis IIIA.
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Ann Clin Transl Neurol. 2023 Jun;10(6):904-917. doi: 10.1002/acn3.51772. Epub 2023 May 11.
Ann Clin Transl Neurol. 2023.
PMID: 37165777
Free PMC article.