rAAV-CFTRΔR Rescues the Cystic Fibrosis Phenotype in Human Intestinal Organoids and Cystic Fibrosis Mice.
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Vidović D, et al. Among authors: de boeck k, de jonge hr.
Am J Respir Crit Care Med. 2016 Feb 1;193(3):288-98. doi: 10.1164/rccm.201505-0914OC.
Am J Respir Crit Care Med. 2016.
PMID: 26509335