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CRISPR medicine for blood disorders: Progress and challenges in delivery.
Mohammadian Gol T, Ureña-Bailén G, Hou Y, Sinn R, Antony JS, Handgretinger R, Mezger M. Mohammadian Gol T, et al. Among authors: urena bailen g. Front Genome Ed. 2023 Jan 6;4:1037290. doi: 10.3389/fgeed.2022.1037290. eCollection 2022. Front Genome Ed. 2023. PMID: 36687779 Free PMC article. Review.
A Mutation-Agnostic Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy.
Antony JS, Daniel-Moreno A, Lamsfus-Calle A, Raju J, Kaftancioglu M, Ureña-Bailén G, Rottenberger J, Hou Y, Santhanakumaran V, Lee JH, Heumos L, Böhringer J, Krägeloh-Mann I, Handgretinger R, Mezger M. Antony JS, et al. Among authors: urena bailen g. CRISPR J. 2022 Feb;5(1):66-79. doi: 10.1089/crispr.2021.0075. Epub 2021 Dec 8. CRISPR J. 2022. PMID: 34882002
Automated Good Manufacturing Practice-Compatible CRISPR-Cas9 Editing of Hematopoietic Stem and Progenitor Cells for Clinical Treatment of β-Hemoglobinopathies.
Ureña-Bailén G, Block M, Grandi T, Aivazidou F, Quednau J, Krenz D, Daniel-Moreno A, Lamsfus-Calle A, Epting T, Handgretinger R, Wild S, Mezger M. Ureña-Bailén G, et al. CRISPR J. 2023 Feb;6(1):5-16. doi: 10.1089/crispr.2022.0086. Epub 2023 Jan 20. CRISPR J. 2023. PMID: 36662546 Free PMC article.
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