Search Page
Save citations to file
Email citations
Send citations to clipboard
Add to Collections
Add to My Bibliography
Create a file for external citation management software
Your saved search
Your RSS Feed
Filters
Results by year
Table representation of search results timeline featuring number of search results per year.
Year | Number of Results |
---|---|
2023 | 1 |
2024 | 5 |
Search Results
6 results
Results by year
Filters applied: . Clear all
Page 1
Reversal of C9orf72 mutation-induced transcriptional dysregulation and pathology in cultured human neurons by allele-specific excision.
Proc Natl Acad Sci U S A. 2024 Apr 23;121(17):e2307814121. doi: 10.1073/pnas.2307814121. Epub 2024 Apr 15.
Proc Natl Acad Sci U S A. 2024.
PMID: 38621131
Free PMC article.
RNA language models predict mutations that improve RNA function.
Shulgina Y, Trinidad MI, Langeberg CJ, Nisonoff H, Chithrananda S, Skopintsev P, Nissley AJ, Patel J, Boger RS, Shi H, Yoon PH, Doherty EE, Pande T, Iyer AM, Doudna JA, Cate JHD.
Shulgina Y, et al.
bioRxiv [Preprint]. 2024 Apr 6:2024.04.05.588317. doi: 10.1101/2024.04.05.588317.
bioRxiv. 2024.
PMID: 38617247
Free PMC article.
Preprint.
Item in Clipboard
Engineering self-deliverable ribonucleoproteins for genome editing in the brain.
Chen K, Stahl EC, Kang MH, Xu B, Allen R, Trinidad M, Doudna JA.
Chen K, et al.
Nat Commun. 2024 Feb 26;15(1):1727. doi: 10.1038/s41467-024-45998-2.
Nat Commun. 2024.
PMID: 38409124
Free PMC article.
Item in Clipboard
Building CRISPR Gene Therapies for the Central Nervous System: A Review.
Salomonsson SE, Clelland CD.
Salomonsson SE, et al.
JAMA Neurol. 2024 Mar 1;81(3):283-290. doi: 10.1001/jamaneurol.2023.4983.
JAMA Neurol. 2024.
PMID: 38285472
Review.
Item in Clipboard
Validated assays for the quantification of C9orf72 human pathology.
Salomonsson SE, Maltos AM, Gill K, Aladesuyi Arogundade O, Brown KA, Sachdev A, Sckaff M, Lam KJK, Fisher IJ, Chouhan RS, Van Laar VS, Marley CB, McLaughlin I, Bankiewicz KS, Tsai YC, Conklin BR, Clelland CD.
Salomonsson SE, et al.
Sci Rep. 2024 Jan 8;14(1):828. doi: 10.1038/s41598-023-50667-3.
Sci Rep. 2024.
PMID: 38191789
Free PMC article.
Item in Clipboard
Lipid Nanoparticles Deliver mRNA to the Brain after an Intracerebral Injection.
Tuma J, Chen YJ, Collins MG, Paul A, Li J, Han H, Sharma R, Murthy N, Lee HY.
Tuma J, et al.
Biochemistry. 2023 Dec 19;62(24):3533-3547. doi: 10.1021/acs.biochem.3c00371. Epub 2023 Sep 20.
Biochemistry. 2023.
PMID: 37729550
Free PMC article.
Item in Clipboard
Cite
Cite