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Table representation of search results timeline featuring number of search results per year.
Year | Number of Results |
---|---|
2012 | 1 |
2013 | 1 |
2015 | 1 |
2016 | 1 |
2017 | 1 |
2023 | 1 |
2024 | 0 |
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Page 1
Antisense oligonucleotide targeting DMPK in patients with myotonic dystrophy type 1: a multicentre, randomised, dose-escalation, placebo-controlled, phase 1/2a trial.
Lancet Neurol. 2023 Mar;22(3):218-228. doi: 10.1016/S1474-4422(23)00001-7.
Lancet Neurol. 2023.
PMID: 36804094
Clinical Trial.
Myotonic dystrophy: approach to therapy.
Thornton CA, Wang E, Carrell EM.
Thornton CA, et al.
Curr Opin Genet Dev. 2017 Jun;44:135-140. doi: 10.1016/j.gde.2017.03.007. Epub 2017 Apr 1.
Curr Opin Genet Dev. 2017.
PMID: 28376341
Free PMC article.
Review.
Item in Clipboard
Dmpk gene deletion or antisense knockdown does not compromise cardiac or skeletal muscle function in mice.
Carrell ST, Carrell EM, Auerbach D, Pandey SK, Bennett CF, Dirksen RT, Thornton CA.
Carrell ST, et al.
Hum Mol Genet. 2016 Oct 1;25(19):4328-4338. doi: 10.1093/hmg/ddw266. Epub 2016 Aug 13.
Hum Mol Genet. 2016.
PMID: 27522499
Free PMC article.
Item in Clipboard
Identification and characterization of modified antisense oligonucleotides targeting DMPK in mice and nonhuman primates for the treatment of myotonic dystrophy type 1.
Pandey SK, Wheeler TM, Justice SL, Kim A, Younis HS, Gattis D, Jauvin D, Puymirat J, Swayze EE, Freier SM, Bennett CF, Thornton CA, MacLeod AR.
Pandey SK, et al.
J Pharmacol Exp Ther. 2015 Nov;355(2):329-40. doi: 10.1124/jpet.115.226969. Epub 2015 Sep 1.
J Pharmacol Exp Ther. 2015.
PMID: 26330536
Free PMC article.
Item in Clipboard
Splicing biomarkers of disease severity in myotonic dystrophy.
Nakamori M, Sobczak K, Puwanant A, Welle S, Eichinger K, Pandya S, Dekdebrun J, Heatwole CR, McDermott MP, Chen T, Cline M, Tawil R, Osborne RJ, Wheeler TM, Swanson MS, Moxley RT 3rd, Thornton CA.
Nakamori M, et al.
Ann Neurol. 2013 Dec;74(6):862-72. doi: 10.1002/ana.23992.
Ann Neurol. 2013.
PMID: 23929620
Free PMC article.
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Targeting nuclear RNA for in vivo correction of myotonic dystrophy.
Wheeler TM, Leger AJ, Pandey SK, MacLeod AR, Nakamori M, Cheng SH, Wentworth BM, Bennett CF, Thornton CA.
Wheeler TM, et al.
Nature. 2012 Aug 2;488(7409):111-5. doi: 10.1038/nature11362.
Nature. 2012.
PMID: 22859208
Free PMC article.
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