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Liver-Directed Adeno-Associated Virus-Mediated Gene Therapy for Mucopolysaccharidosis Type VI.
Brunetti-Pierri N, Ferla R, Ginocchio VM, Rossi A, Fecarotta S, Romano R, Parenti G, Yildiz Y, Zancan S, Pecorella V, Dell'Anno M, Graziano M, Alliegro M, Andria G, Santamaria F, Brunetti-Pierri R, Simonelli F, Nigro V, Vargas M, Servillo G, Borgia F, Soscia E, Gargaro M, Funghini S, Tedesco N, Le Brun PR, Rupar CA, Prasad C, O'Callaghan M, Mitchell JJ, Danos O, Marteau JB, Galimberti S, Valsecchi MG, Veron P, Mingozzi F, Fallarino F, la Marca G, Sivri HS, Auricchio A. Brunetti-Pierri N, et al. Among authors: tedesco n. NEJM Evid. 2022 Jul;1(7):EVIDoa2200052. doi: 10.1056/EVIDoa2200052. Epub 2022 Jun 6. NEJM Evid. 2022. PMID: 38319253
Efficacy, pharmacokinetics, and safety in the mouse and primate retina of dual AAV vectors for Usher syndrome type 1B.
Ferla R, Dell'Aquila F, Doria M, Ferraiuolo M, Noto A, Grazioli F, Ammendola V, Testa F, Melillo P, Iodice C, Risca G, Tedesco N, le Brun PR, Surace EM, Simonelli F, Galimberti S, Valsecchi MG, Marteau JB, Veron P, Colloca S, Auricchio A. Ferla R, et al. Among authors: tedesco n. Mol Ther Methods Clin Dev. 2023 Feb 11;28:396-411. doi: 10.1016/j.omtm.2023.02.002. eCollection 2023 Mar 9. Mol Ther Methods Clin Dev. 2023. PMID: 36910588 Free PMC article.
Enhancing the Therapeutic Potential of Sulfamidase for the Treatment of Mucopolysaccharidosis IIIA.
Sorrentino NC, Cacace V, De Risi M, Maffia V, Strollo S, Tedesco N, Nusco E, Romagnoli N, Ventrella D, Huang Y, Liu N, Kalled SL, Choi VW, De Leonibus E, Fraldi A. Sorrentino NC, et al. Among authors: tedesco n. Mol Ther Methods Clin Dev. 2019 Oct 28;15:333-342. doi: 10.1016/j.omtm.2019.10.009. eCollection 2019 Dec 13. Mol Ther Methods Clin Dev. 2019. PMID: 31788497 Free PMC article.
The Musculoskeletal Tumor Society Clinical Practice Guideline on the Management of Metastatic Humeral Disease.
Tedesco NS, Mesko N, Wodajo F; Management of Metastatic Humeral Disease Work Group; Staff of the American Academy of Orthopaedic Surgeons and the Musculoskeletal Tumor Society; Management of Metastatic Humeral Disease Work Group and Staff of the American Academy of Orthopaedic Surgeons and the Musculoskeletal Tumor Society. Tedesco NS, et al. J Am Acad Orthop Surg. 2024 May 15;32(10):e482-e488. doi: 10.5435/JAAOS-D-24-00053. Epub 2024 Mar 5. J Am Acad Orthop Surg. 2024. PMID: 38442357
PNPLA3 Risk Allele Association With ALT Response to Semaglutide Treatment.
Urias E, Tedesco NR, Oliveri A, Raut C; Michigan Genomics Initiative; Speliotes EK, Chen VL. Urias E, et al. Among authors: tedesco nr. Gastroenterology. 2024 Mar;166(3):515-517.e2. doi: 10.1053/j.gastro.2023.11.018. Epub 2023 Nov 14. Gastroenterology. 2024. PMID: 37972824 Free article. No abstract available.
32 results