AAV-mediated editing of PMP22 rescues Charcot-Marie-Tooth disease type 1A features in patient-derived iPS Schwann cells.
Yoshioka Y, Taniguchi JB, Homma H, Tamura T, Fujita K, Inotsume M, Tagawa K, Misawa K, Matsumoto N, Nakagawa M, Inoue H, Tanaka H, Okazawa H.
Yoshioka Y, et al. Among authors: taniguchi jb.
Commun Med (Lond). 2023 Nov 28;3(1):170. doi: 10.1038/s43856-023-00400-y.
Commun Med (Lond). 2023.
PMID: 38017287
Free PMC article.