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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
2006 2
2007 2
2008 1
2009 2
2010 3
2011 7
2012 4
2013 7
2014 3
2015 4
2016 12
2017 5
2018 8
2019 2
2020 8
2021 13
2022 5
2023 12
2024 2

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88 results

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Page 1
Intrathecal Gene Therapy for Giant Axonal Neuropathy.
Bharucha-Goebel DX, Todd JJ, Saade D, Norato G, Jain M, Lehky T, Bailey RM, Chichester JA, Calcedo R, Armao D, Foley AR, Mohassel P, Tesfaye E, Carlin BP, Seremula B, Waite M, Zein WM, Huryn LA, Crawford TO, Sumner CJ, Hoke A, Heiss JD, Charnas L, Hooper JE, Bouldin TW, Kang EM, Rybin D, Gray SJ, Bönnemann CG; GAN Trial Team. Bharucha-Goebel DX, et al. Among authors: gray sj. N Engl J Med. 2024 Mar 21;390(12):1092-1104. doi: 10.1056/NEJMoa2307952. N Engl J Med. 2024. PMID: 38507752
AAV-based in vivo gene therapy for neurological disorders.
Ling Q, Herstine JA, Bradbury A, Gray SJ. Ling Q, et al. Among authors: gray sj. Nat Rev Drug Discov. 2023 Oct;22(10):789-806. doi: 10.1038/s41573-023-00766-7. Epub 2023 Sep 1. Nat Rev Drug Discov. 2023. PMID: 37658167 Review.
Long-term safety and dose escalation of intracerebroventricular CLN5 gene therapy in sheep supports clinical translation for CLN5 Batten disease.
Mitchell NL, Murray SJ, Wellby MP, Barrell GK, Russell KN, Deane AR, Wynyard JR, Palmer MJ, Pulickan A, Prendergast PM, Casy W, Gray SJ, Palmer DN. Mitchell NL, et al. Among authors: gray sj. Front Genet. 2023 Aug 8;14:1212228. doi: 10.3389/fgene.2023.1212228. eCollection 2023. Front Genet. 2023. PMID: 37614821 Free PMC article.
88 results