Novel approach to idursulfase and laronidase desensitization in type 2 and type 1 S mucopolysaccharidosis (MPS).
Spataro F, Viggiani F, Macchia DG, Rollo V, Tummolo A, Suppressa P, Sabba' C, Rossi MP, Giliberti L, Satriano F, Nettis E, Di Bona D, Caiaffa MF, Fischetto R, Macchia L.
Spataro F, et al.
Orphanet J Rare Dis. 2022 Nov 3;17(1):402. doi: 10.1186/s13023-022-02556-7.
Orphanet J Rare Dis. 2022.
PMID: 36329518
Free PMC article.