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A Novel MYCN-Specific Antigene Oligonucleotide Deregulates Mitochondria and Inhibits Tumor Growth in MYCN-Amplified Neuroblastoma.
Cancer Res. 2019 Dec 15;79(24):6166-6177. doi: 10.1158/0008-5472.CAN-19-0008. Epub 2019 Oct 15.
Cancer Res. 2019.
PMID: 31615807
Compound heterozygosity for two different amino-acid substitution mutations in the thrombopoietin receptor (c-mpl gene) in congenital amegakaryocytic thrombocytopenia (CAMT).
Tonelli R, Scardovi AL, Pession A, Strippoli P, Bonsi L, Vitale L, Prete A, Locatelli F, Bagnara GP, Paolucci G.
Tonelli R, et al. Among authors: scardovi al.
Hum Genet. 2000 Sep;107(3):225-33. doi: 10.1007/s004390000357.
Hum Genet. 2000.
PMID: 11071383
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The MYCN inhibitor BGA002 restores the retinoic acid response leading to differentiation or apoptosis by the mTOR block in MYCN-amplified neuroblastoma.
Lampis S, Raieli S, Montemurro L, Bartolucci D, Amadesi C, Bortolotti S, Angelucci S, Scardovi AL, Nieddu G, Cerisoli L, Paganelli F, Valente S, Fischer M, Martelli AM, Pasquinelli G, Pession A, Hrelia P, Tonelli R.
Lampis S, et al. Among authors: scardovi al.
J Exp Clin Cancer Res. 2022 Apr 30;41(1):160. doi: 10.1186/s13046-022-02367-5.
J Exp Clin Cancer Res. 2022.
PMID: 35490242
Free PMC article.
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Antigene MYCN Silencing by BGA002 Inhibits SCLC Progression Blocking mTOR Pathway and Overcomes Multidrug Resistance.
Bortolotti S, Angelucci S, Montemurro L, Bartolucci D, Raieli S, Lampis S, Amadesi C, Scardovi A, Nieddu G, Cerisoli L, Paganelli F, Chiarini F, Teti G, Falconi M, Pession A, Hrelia P, Tonelli R.
Bortolotti S, et al.
Cancers (Basel). 2023 Feb 3;15(3):990. doi: 10.3390/cancers15030990.
Cancers (Basel). 2023.
PMID: 36765949
Free PMC article.
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