Targeting ON-bipolar cells by AAV gene therapy stably reverses LRIT3-congenital stationary night blindness.
Miyadera K, Santana E, Roszak K, Iffrig S, Visel M, Iwabe S, Boyd RF, Bartoe JT, Sato Y, Gray A, Ripolles-Garcia A, Dufour VL, Byrne LC, Flannery JG, Beltran WA, Aguirre GD.
Miyadera K, et al. Among authors: santana e.
Proc Natl Acad Sci U S A. 2022 Mar 29;119(13):e2117038119. doi: 10.1073/pnas.2117038119. Epub 2022 Mar 22.
Proc Natl Acad Sci U S A. 2022.
PMID: 35316139
Free PMC article.