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Longitudinal changes of swallowing safety and efficiency in infants with spinal muscular atrophy who received disease modifying therapies.
Pediatr Pulmonol. 2024 May;59(5):1364-1371. doi: 10.1002/ppul.26919. Epub 2024 Feb 15.
Pediatr Pulmonol. 2024.
PMID: 38358081
Thrombotic microangiopathy following systemic AAV administration is dependent on anti-capsid antibodies.
Salabarria SM, Corti M, Coleman KE, Wichman MB, Berthy JA, D'Souza P, Tifft CJ, Herzog RW, Elder ME, Shoemaker LR, Leon-Astudillo C, Tavakkoli F, Kirn DH, Schwartz JD, Byrne BJ.
Salabarria SM, et al.
J Clin Invest. 2024 Jan 2;134(1):e173510. doi: 10.1172/JCI173510.
J Clin Invest. 2024.
PMID: 37988172
Free PMC article.
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Polysomnography findings in children with spinal muscular atrophy after onasemnogene-abeparvovec.
Leon-Astudillo C, Wagner M, Salabarria SM, Lammers J, Berthy J, Zingariello CD, Byrne BJ, Smith BK.
Leon-Astudillo C, et al. Among authors: salabarria sm.
Sleep Med. 2023 Jan;101:234-237. doi: 10.1016/j.sleep.2022.11.006. Epub 2022 Nov 10.
Sleep Med. 2023.
PMID: 36442421
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Advancements in AAV-mediated Gene Therapy for Pompe Disease.
Salabarria SM, Nair J, Clement N, Smith BK, Raben N, Fuller DD, Byrne BJ, Corti M.
Salabarria SM, et al.
J Neuromuscul Dis. 2020;7(1):15-31. doi: 10.3233/JND-190426.
J Neuromuscul Dis. 2020.
PMID: 31796685
Free PMC article.
Review.
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