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Targeting photoreceptors via intravitreal delivery using novel, capsid-mutated AAV vectors.
PLoS One. 2013 Apr 26;8(4):e62097. doi: 10.1371/journal.pone.0062097. Print 2013.
PLoS One. 2013.
PMID: 23637972
Free PMC article.
A comprehensive review of retinal gene therapy.
Boye SE, Boye SL, Lewin AS, Hauswirth WW.
Boye SE, et al.
Mol Ther. 2013 Mar;21(3):509-19. doi: 10.1038/mt.2012.280. Epub 2013 Jan 29.
Mol Ther. 2013.
PMID: 23358189
Free PMC article.
Review.
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