Pratt MA - Search Results

1

AAV9 Gene Therapy Increases Lifespan and Treats Pathological and Behavioral Abnormalities in a Mouse Model of CLN8-Batten Disease.

Johnson TB, White KA, Brudvig JJ, Cain JT, Langin L, Pratt MA, Booth CD, Timm DJ, Davis SS, Meyerink B, Likhite S, Meyer K, Weimer JM. Johnson TB, et al. Among authors: pratt ma. Mol Ther. 2021 Jan 6;29(1):162-175. doi: 10.1016/j.ymthe.2020.09.033. Epub 2020 Sep 24. Mol Ther. 2021. PMID: 33010819 Free PMC article.

2

Intracranial delivery of AAV9 gene therapy partially prevents retinal degeneration and visual deficits in CLN6-Batten disease mice.

White KA, Nelvagal HR, Poole TA, Lu B, Johnson TB, Davis S, Pratt MA, Brudvig J, Assis AB, Likhite S, Meyer K, Kaspar BK, Cooper JD, Wang S, Weimer JM. White KA, et al. Among authors: pratt ma. Mol Ther Methods Clin Dev. 2021 Jan 5;20:497-507. doi: 10.1016/j.omtm.2020.12.014. eCollection 2021 Mar 12. Mol Ther Methods Clin Dev. 2021. PMID: 33665223 Free PMC article.

3

Glycerophosphoinositol is Elevated in Blood Samples From CLN3 ^Δex7-8 pigs, Cln3 ^Δex7-8 Mice, and CLN3-Affected Individuals.

Brudvig JJ, Swier VJ, Johnson TB, Cain JC, Pratt M, Rechtzigel M, Leppert H, Dang Do AN, Porter FD, Weimer JM. Brudvig JJ, et al. Biomark Insights. 2022 Jun 19;17:11772719221107765. doi: 10.1177/11772719221107765. eCollection 2022. Biomark Insights. 2022. PMID: 36212622 Free PMC article.

4

Sex-split analysis of pathology and motor-behavioral outcomes in a mouse model of CLN8-Batten disease reveals an increased disease burden and trajectory in female Cln8^mnd mice.

Holmes AD, White KA, Pratt MA, Johnson TB, Likhite S, Meyer K, Weimer JM. Holmes AD, et al. Among authors: pratt ma. Orphanet J Rare Dis. 2022 Nov 11;17(1):411. doi: 10.1186/s13023-022-02564-7. Orphanet J Rare Dis. 2022. PMID: 36369162 Free PMC article.

5

Early postnatal administration of an AAV9 gene therapy is safe and efficacious in CLN3 disease.

Johnson TB, Brudvig JJ, Likhite S, Pratt MA, White KA, Cain JT, Booth CD, Timm DJ, Davis SS, Meyerink B, Pineda R, Dennys-Rivers C, Kaspar BK, Meyer K, Weimer JM. Johnson TB, et al. Among authors: pratt ma. Front Genet. 2023 Mar 24;14:1118649. doi: 10.3389/fgene.2023.1118649. eCollection 2023. Front Genet. 2023. PMID: 37035740 Free PMC article.

6

Protracted CLN3 Batten disease in mice that genetically model an exon-skipping therapeutic approach.

Centa JL, Stratton MP, Pratt MA, Osterlund Oltmanns JR, Wallace DG, Miller SA, Weimer JM, Hastings ML. Centa JL, et al. Among authors: pratt ma. Mol Ther Nucleic Acids. 2023 Jun 3;33:15-27. doi: 10.1016/j.omtn.2023.05.025. eCollection 2023 Sep 12. Mol Ther Nucleic Acids. 2023. PMID: 37359347 Free PMC article.

7

Sortilin inhibition treats multiple neurodegenerative lysosomal storage disorders.

Leppert HG, Anderson JT, Timm KJ, Davoli C, Pratt MA, Booth CD, White KA, Rechtzigel MJ, Meyerink BL, Johnson TB, Brudvig JJ, Weimer JM. Leppert HG, et al. Among authors: pratt ma. bioRxiv [Preprint]. 2023 Sep 22:2023.09.22.559064. doi: 10.1101/2023.09.22.559064. bioRxiv. 2023. PMID: 37790379 Free PMC article. Preprint.

8

Induction of alternative NF-κB within TAg-induced basal mammary tumors in activation-resistant inhibitor of κ-B kinase (IKKα) mutant mice.

Ould-Brahim F, Sau A, Carr DA, Jiang T, Pratt MAC. Ould-Brahim F, et al. Among authors: pratt mac. Tumour Biol. 2022;44(1):187-203. doi: 10.3233/TUB-220006. Tumour Biol. 2022. PMID: 36093651 Free article.

9

Multiple roles for Bcl-3 in mammary gland branching, stromal collagen invasion, involution and tumor pathology.

Carr D, Zein A, Coulombe J, Jiang T, Cabrita MA, Ward G, Daneshmand M, Sau A, Pratt MAC. Carr D, et al. Among authors: pratt mac. Breast Cancer Res. 2022 Jun 9;24(1):40. doi: 10.1186/s13058-022-01536-w. Breast Cancer Res. 2022. PMID: 35681213 Free PMC article.

10

Intrinsically Disordered SRC-3/AIB1 Protein Undergoes Homeostatic Nuclear Extrusion by Nuclear Budding While Ectopic Expression Induces Nucleophagy.

Cabrita MA, Renart LI, Lau R, Pratt MAC. Cabrita MA, et al. Among authors: pratt mac. Cells. 2019 Oct 19;8(10):1278. doi: 10.3390/cells8101278. Cells. 2019. PMID: 31635050 Free PMC article.

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