Novel Exon-Skipping Therapeutic Approach for the DMD Gene Based on Asymptomatic Deletions of Exon 49.
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Abaji M, et al. Among authors: philip n.
Genes (Basel). 2022 Jul 19;13(7):1277. doi: 10.3390/genes13071277.
Genes (Basel). 2022.
PMID: 35886062
Free PMC article.