Ionizable lipid nanoparticles deliver mRNA to pancreatic β cells via macrophage-mediated gene transfer.
Melamed JR, Yerneni SS, Arral ML, LoPresti ST, Chaudhary N, Sehrawat A, Muramatsu H, Alameh MG, Pardi N, Weissman D, Gittes GK, Whitehead KA.
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Sci Adv. 2023 Jan 27;9(4):eade1444. doi: 10.1126/sciadv.ade1444. Epub 2023 Jan 27.
Sci Adv. 2023.
PMID: 36706177
Free PMC article.