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Volumetric study of brain MRI in a cohort of patients with neurotransmitter disorders.
Neuroradiology. 2022 Nov;64(11):2179-2190. doi: 10.1007/s00234-022-02989-8. Epub 2022 Jun 4.
Neuroradiology. 2022.
PMID: 35662359
Eculizumab in refractory generalized myasthenia gravis previously treated with rituximab: subgroup analysis of REGAIN and its extension study.
Siddiqi ZA, Nowak RJ, Mozaffar T, O'Brien F, Yountz M, Patti F; REGAIN Study Group.
Siddiqi ZA, et al.
Muscle Nerve. 2021 Dec;64(6):662-669. doi: 10.1002/mus.27422. Epub 2021 Oct 14.
Muscle Nerve. 2021.
PMID: 34590717
Clinical Trial.
Item in Clipboard
Post-intervention Status in Patients With Refractory Myasthenia Gravis Treated With Eculizumab During REGAIN and Its Open-Label Extension.
Mantegazza R, Wolfe GI, Muppidi S, Wiendl H, Fujita KP, O'Brien FL, Booth HDE, Howard JF Jr; REGAIN Study Group.
Mantegazza R, et al.
Neurology. 2021 Jan 26;96(4):e610-e618. doi: 10.1212/WNL.0000000000011207. Epub 2020 Nov 23.
Neurology. 2021.
PMID: 33229455
Free PMC article.
Clinical Trial.
Item in Clipboard
'Minimal symptom expression' in patients with acetylcholine receptor antibody-positive refractory generalized myasthenia gravis treated with eculizumab.
Vissing J, Jacob S, Fujita KP, O'Brien F, Howard JF; REGAIN study group.
Vissing J, et al.
J Neurol. 2020 Jul;267(7):1991-2001. doi: 10.1007/s00415-020-09770-y. Epub 2020 Mar 18.
J Neurol. 2020.
PMID: 32189108
Free PMC article.
Clinical Trial.
Item in Clipboard
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy.
Finkel RS, Mercuri E, Darras BT, Connolly AM, Kuntz NL, Kirschner J, Chiriboga CA, Saito K, Servais L, Tizzano E, Topaloglu H, Tulinius M, Montes J, Glanzman AM, Bishop K, Zhong ZJ, Gheuens S, Bennett CF, Schneider E, Farwell W, De Vivo DC; ENDEAR Study Group.
Finkel RS, et al.
N Engl J Med. 2017 Nov 2;377(18):1723-1732. doi: 10.1056/NEJMoa1702752.
N Engl J Med. 2017.
PMID: 29091570
Free article.
Clinical Trial.
Item in Clipboard
Safety and efficacy of eculizumab in anti-acetylcholine receptor antibody-positive refractory generalised myasthenia gravis (REGAIN): a phase 3, randomised, double-blind, placebo-controlled, multicentre study.
Howard JF Jr, Utsugisawa K, Benatar M, Murai H, Barohn RJ, Illa I, Jacob S, Vissing J, Burns TM, Kissel JT, Muppidi S, Nowak RJ, O'Brien F, Wang JJ, Mantegazza R; REGAIN Study Group.
Howard JF Jr, et al.
Lancet Neurol. 2017 Dec;16(12):976-986. doi: 10.1016/S1474-4422(17)30369-1. Epub 2017 Oct 20.
Lancet Neurol. 2017.
PMID: 29066163
Clinical Trial.
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