GP64-pseudotyped lentiviral vectors target liver endothelial cells and correct hemophilia A mice.
Milani M, Canepari C, Assanelli S, Merlin S, Borroni E, Starinieri F, Biffi M, Russo F, Fabiano A, Zambroni D, Annoni A, Naldini L, Follenzi A, Cantore A.
Milani M, et al.
EMBO Mol Med. 2024 Apr 29. doi: 10.1038/s44321-024-00072-8. Online ahead of print.
EMBO Mol Med. 2024.
PMID: 38684862
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