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Preclinical development and qualification of ZFN-mediated CCR5 disruption in human hematopoietic stem/progenitor cells.
DiGiusto DL, Cannon PM, Holmes MC, Li L, Rao A, Wang J, Lee G, Gregory PD, Kim KA, Hayward SB, Meyer K, Exline C, Lopez E, Henley J, Gonzalez N, Bedell V, Stan R, Zaia JA. DiGiusto DL, et al. Among authors: meyer k. Mol Ther Methods Clin Dev. 2016 Nov 9;3:16067. doi: 10.1038/mtm.2016.67. eCollection 2016. Mol Ther Methods Clin Dev. 2016. PMID: 27900346 Free PMC article.
Dose-Dependent Prevention of Metabolic and Neurologic Disease in Murine MPS II by ZFN-Mediated In Vivo Genome Editing.
Laoharawee K, DeKelver RC, Podetz-Pedersen KM, Rohde M, Sproul S, Nguyen HO, Nguyen T, St Martin SJ, Ou L, Tom S, Radeke R, Meyer KE, Holmes MC, Whitley CB, Wechsler T, McIvor RS. Laoharawee K, et al. Among authors: meyer ke. Mol Ther. 2018 Apr 4;26(4):1127-1136. doi: 10.1016/j.ymthe.2018.03.002. Epub 2018 Mar 10. Mol Ther. 2018. PMID: 29580682 Free PMC article.
ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome.
Ou L, DeKelver RC, Rohde M, Tom S, Radeke R, St Martin SJ, Santiago Y, Sproul S, Przybilla MJ, Koniar BL, Podetz-Pedersen KM, Laoharawee K, Cooksley RD, Meyer KE, Holmes MC, McIvor RS, Wechsler T, Whitley CB. Ou L, et al. Among authors: meyer ke. Mol Ther. 2019 Jan 2;27(1):178-187. doi: 10.1016/j.ymthe.2018.10.018. Epub 2018 Nov 1. Mol Ther. 2019. PMID: 30528089 Free PMC article.
AAV2/6 Gene Therapy in a Murine Model of Fabry Disease Results in Supraphysiological Enzyme Activity and Effective Substrate Reduction.
Yasuda M, Huston MW, Pagant S, Gan L, St Martin S, Sproul S, Richards D, Ballaron S, Hettini K, Ledeboer A, Falese L, Cao L, Lu Y, Holmes MC, Meyer K, Desnick RJ, Wechsler T. Yasuda M, et al. Among authors: meyer k. Mol Ther Methods Clin Dev. 2020 Jul 9;18:607-619. doi: 10.1016/j.omtm.2020.07.002. eCollection 2020 Sep 11. Mol Ther Methods Clin Dev. 2020. PMID: 32775495 Free PMC article.
A robust and flexible baculovirus-insect cell system for AAV vector production with improved yield, capsid ratios and potency.
Marwidi Y, Nguyen HB, Santos D, Wangzor T, Bhardwaj S, Ernie G, Prawdzik G, Lew G, Shivak D, Trias M, Padilla J, Tran H, Meyer K, Surosky R, Ward AM. Marwidi Y, et al. Among authors: meyer k. Mol Ther Methods Clin Dev. 2024 Mar 4;32(2):101228. doi: 10.1016/j.omtm.2024.101228. eCollection 2024 Jun 13. Mol Ther Methods Clin Dev. 2024. PMID: 38524756 Free PMC article.
CERE-120 Prevents Irradiation-Induced Hypofunction and Restores Immune Homeostasis in Porcine Salivary Glands.
Lombaert IMA, Patel VN, Jones CE, Villier DC, Canada AE, Moore MR, Berenstein E, Zheng C, Goldsmith CM, Chorini JA, Martin D, Zourelias L, Trombetta MG, Edwards PC, Meyer K, Ando D, Passineau MJ, Hoffman MP. Lombaert IMA, et al. Among authors: meyer k. Mol Ther Methods Clin Dev. 2020 Jul 31;18:839-855. doi: 10.1016/j.omtm.2020.07.016. eCollection 2020 Sep 11. Mol Ther Methods Clin Dev. 2020. PMID: 32953934 Free PMC article.
Gene Editing: Regulatory and Translation to Clinic.
Ando D, Meyer K. Ando D, et al. Among authors: meyer k. Hematol Oncol Clin North Am. 2017 Oct;31(5):797-808. doi: 10.1016/j.hoc.2017.06.002. Hematol Oncol Clin North Am. 2017. PMID: 28895848 Review.
2,908 results