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Year | Number of Results |
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2019 | 1 |
2021 | 1 |
2022 | 1 |
2023 | 2 |
2024 | 1 |
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Page 1
Clinical Effectiveness of Newborn Screening for Spinal Muscular Atrophy: A Nonrandomized Controlled Trial.
JAMA Pediatr. 2024 Apr 8:e240492. doi: 10.1001/jamapediatrics.2024.0492. Online ahead of print.
JAMA Pediatr. 2024.
PMID: 38587854
Fungal Gut Microbiome in Myasthenia Gravis: A Sub-Analysis of the MYBIOM Study.
Verhasselt HL, Ramakrishnan E, Schlag M, Marchesi JR, Buer J, Kleinschnitz C, Hagenacker T, Totzeck A.
Verhasselt HL, et al. Among authors: schlag m.
J Fungi (Basel). 2023 May 13;9(5):569. doi: 10.3390/jof9050569.
J Fungi (Basel). 2023.
PMID: 37233280
Free PMC article.
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Improvements in Walking Distance during Nusinersen Treatment - A Prospective 3-year SMArtCARE Registry Study.
Pechmann A, Behrens M, Dörnbrack K, Tassoni A, Wenzel F, Stein S, Vogt S, Zöller D, Bernert G, Hagenacker T, Schara-Schmidt U, Walter MC, Steinbach M, Blaschek A, Baumann M, Baumgartner M, Becker B, Flotats-Bastardas M, Friese J, Günther R, Hahn A, Küpper H, Johannsen J, Kamm C, Koch JC, Köhler C, Kölbel H, Kolzter K, von Moers A, Naegel S, Neuwirth C, Petri S, Rödiger A, Schimmel M, Schrank B, Schreiber G, Smitka M, Stadler C, Steiner E, Stögmann E, Trollmann R, Türk M, Weiler M, Stoltenburg C, Willichowsky E, Zeller D, Ziegler A, Lochmüller H, Kirschner J; SMArtCARE Study Group.
Pechmann A, et al.
J Neuromuscul Dis. 2023;10(1):29-40. doi: 10.3233/JND-221600.
J Neuromuscul Dis. 2023.
PMID: 36565133
Free PMC article.
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Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study.
Pechmann A, Behrens M, Dörnbrack K, Tassoni A, Wenzel F, Stein S, Vogt S, Zöller D, Bernert G, Hagenacker T, Schara-Schmidt U, Walter MC, Bertsche A, Vill K, Baumann M, Baumgartner M, Cordts I, Eisenkölbl A, Flotats-Bastardas M, Friese J, Günther R, Hahn A, Horber V, Husain RA, Illsinger S, Jahnel J, Johannsen J, Köhler C, Kölbel H, Müller M, von Moers A, Schwerin-Nagel A, Reihle C, Schlachter K, Schreiber G, Schwartz O, Smitka M, Steiner E, Trollmann R, Weiler M, Weiß C, Wiegand G, Wilichowski E, Ziegler A, Lochmüller H, Kirschner J; SMArtCARE study group.
Pechmann A, et al.
Orphanet J Rare Dis. 2022 Oct 23;17(1):384. doi: 10.1186/s13023-022-02547-8.
Orphanet J Rare Dis. 2022.
PMID: 36274155
Free PMC article.
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Gut bacterial microbiota in patients with myasthenia gravis: results from the MYBIOM study.
Totzeck A, Ramakrishnan E, Schlag M, Stolte B, Kizina K, Bolz S, Thimm A, Stettner M, Marchesi JR, Buer J, Kleinschnitz C, Verhasselt HL, Hagenacker T.
Totzeck A, et al. Among authors: schlag m.
Ther Adv Neurol Disord. 2021 Aug 11;14:17562864211035657. doi: 10.1177/17562864211035657. eCollection 2021.
Ther Adv Neurol Disord. 2021.
PMID: 34394728
Free PMC article.
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Neurofilament Heavy Chain and Tau Protein Are Not Elevated in Cerebrospinal Fluid of Adult Patients with Spinal Muscular Atrophy during Loading with Nusinersen.
Totzeck A, Stolte B, Kizina K, Bolz S, Schlag M, Thimm A, Kleinschnitz C, Hagenacker T.
Totzeck A, et al. Among authors: schlag m.
Int J Mol Sci. 2019 Oct 30;20(21):5397. doi: 10.3390/ijms20215397.
Int J Mol Sci. 2019.
PMID: 31671515
Free PMC article.
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