Matzner U - Search Results

1

Neurodegenerative disease after hematopoietic stem cell transplantation in metachromatic leukodystrophy.

Al-Saady M, Beerepoot S, Plug BC, Breur M, Galabova H, Pouwels PJW, Boelens JJ, Lindemans C, van Hasselt PM, Matzner U, Vanderver A, Bugiani M, van der Knaap MS, Wolf NI. Al-Saady M, et al. Among authors: matzner u. Ann Clin Transl Neurol. 2023 Jul;10(7):1146-1159. doi: 10.1002/acn3.51796. Epub 2023 May 22. Ann Clin Transl Neurol. 2023. PMID: 37212343 Free PMC article.

2

Metachromatic leukodystrophy and transplantation: remyelination, no cross-correction.

Wolf NI, Breur M, Plug B, Beerepoot S, Westerveld ASR, van Rappard DF, de Vries SI, Kole MHP, Vanderver A, van der Knaap MS, Lindemans CA, van Hasselt PM, Boelens JJ, Matzner U, Gieselmann V, Bugiani M. Wolf NI, et al. Among authors: matzner u. Ann Clin Transl Neurol. 2020 Feb;7(2):169-180. doi: 10.1002/acn3.50975. Epub 2020 Jan 22. Ann Clin Transl Neurol. 2020. PMID: 31967741 Free PMC article.

3

Gene therapy of metachromatic leukodystrophy.

Matzner U, Gieselmann V. Matzner U, et al. Expert Opin Biol Ther. 2005 Jan;5(1):55-65. doi: 10.1517/14712598.5.1.55. Expert Opin Biol Ther. 2005. PMID: 15709909 Review.

4

Efficacy of enzyme replacement therapy in an aggravated mouse model of metachromatic leukodystrophy declines with age.

Matthes F, Stroobants S, Gerlach D, Wohlenberg C, Wessig C, Fogh J, Gieselmann V, Eckhardt M, D'Hooge R, Matzner U. Matthes F, et al. Among authors: matzner u. Hum Mol Genet. 2012 Jun 1;21(11):2599-609. doi: 10.1093/hmg/dds086. Epub 2012 Mar 2. Hum Mol Genet. 2012. PMID: 22388935

5

Enzyme replacement therapy of a novel humanized mouse model of globoid cell leukodystrophy.

Matthes F, Andersson C, Stein A, Eistrup C, Fogh J, Gieselmann V, Wenger DA, Matzner U. Matthes F, et al. Among authors: matzner u. Exp Neurol. 2015 Sep;271:36-45. doi: 10.1016/j.expneurol.2015.04.020. Epub 2015 May 6. Exp Neurol. 2015. PMID: 25956830

6

Arylsulfatase A Overexpressing Human iPSC-derived Neural Cells Reduce CNS Sulfatide Storage in a Mouse Model of Metachromatic Leukodystrophy.

Doerr J, Böckenhoff A, Ewald B, Ladewig J, Eckhardt M, Gieselmann V, Matzner U, Brüstle O, Koch P. Doerr J, et al. Among authors: matzner u. Mol Ther. 2015 Sep;23(9):1519-31. doi: 10.1038/mt.2015.106. Epub 2015 Jun 10. Mol Ther. 2015. PMID: 26061647 Free PMC article.

7

Evolutionary redesign of the lysosomal enzyme arylsulfatase A increases efficacy of enzyme replacement therapy for metachromatic leukodystrophy.

Simonis H, Yaghootfam C, Sylvester M, Gieselmann V, Matzner U. Simonis H, et al. Among authors: matzner u. Hum Mol Genet. 2019 Jun 1;28(11):1810-1821. doi: 10.1093/hmg/ddz020. Hum Mol Genet. 2019. PMID: 30657900

8

Engineered arylsulfatase A with increased activity, stability and brain delivery for therapy of metachromatic leukodystrophy.

Yaghootfam C, Sylvester M, Turk B, Gieselmann V, Matzner U. Yaghootfam C, et al. Among authors: matzner u. Mol Ther. 2023 Oct 4;31(10):2962-2974. doi: 10.1016/j.ymthe.2023.08.019. Epub 2023 Aug 29. Mol Ther. 2023. PMID: 37644722

9

Enzyme replacement improves nervous system pathology and function in a mouse model for metachromatic leukodystrophy.

Matzner U, Herbst E, Hedayati KK, Lüllmann-Rauch R, Wessig C, Schröder S, Eistrup C, Möller C, Fogh J, Gieselmann V. Matzner U, et al. Hum Mol Genet. 2005 May 1;14(9):1139-52. doi: 10.1093/hmg/ddi126. Epub 2005 Mar 16. Hum Mol Genet. 2005. PMID: 15772092

10

Induction of tolerance to human arylsulfatase A in a mouse model of metachromatic leukodystrophy.

Matzner U, Matthes F, Herbst E, Lüllmann-Rauch R, Callaerts-Vegh Z, D'Hooge R, Weigelt C, Eistrup C, Fogh J, Gieselmann V. Matzner U, et al. Mol Med. 2007 Sep-Oct;13(9-10):471-9. doi: 10.2119/2007-00063.Matzner. Mol Med. 2007. PMID: 17660863 Free PMC article.

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