Effects of Chronic, Maximal Phosphorodiamidate Morpholino Oligomer (PMO) Dosing on Muscle Function and Dystrophin Restoration in a Mouse Model of Duchenne Muscular Dystrophy.
Benny Klimek ME, Vila MC, Edwards K, Boehler J, Novak J, Zhang A, Van der Meulen J, Tatum K, Quinn J, Fiorillo A, Burki U, Straub V, Lu QL, Hathout Y, van Den Anker J, Partridge TA, Morales M, Hoffman E, Nagaraju K.
Benny Klimek ME, et al. Among authors: lu ql.
J Neuromuscul Dis. 2021;8(s2):S369-S381. doi: 10.3233/JND-210701.
J Neuromuscul Dis. 2021.
PMID: 34569970