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Laryngeal, Tracheal, and Bronchial Disease in the Mucopolysaccharidoses: Endoscopic Study.
Diagnostics (Basel). 2020 Jan 10;10(1):37. doi: 10.3390/diagnostics10010037.
Diagnostics (Basel). 2020.
PMID: 31936731
Free PMC article.
Alternative laronidase dose regimen for patients with mucopolysaccharidosis I: a multinational, retrospective, chart review case series.
Horovitz DD, Acosta AX, Giugliani R, Hlavatá A, Hlavatá K, Tchan MC, Lopes Barth A, Cardoso L Jr, Embiruçu de Araújo Leão EK, Esposito AC, Kyosen SO, De Souza CF, Martins AM.
Horovitz DD, et al. Among authors: lopes barth a.
Orphanet J Rare Dis. 2016 Apr 29;11(1):51. doi: 10.1186/s13023-016-0437-8.
Orphanet J Rare Dis. 2016.
PMID: 27129473
Free PMC article.
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