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Page 1
Brain ventricular enlargement in human and murine acute intermittent porphyria.
Jericó D, Luis EO, Cussó L, Fernández-Seara MA, Morales X, Córdoba KM, Benito M, Sampedro A, Larriva M, Ramírez MJ, de Salamanca RE, Ortiz-de-Solorzano C, Alegre M, Prieto J, Lanciego JL, D'Avola D, González-Aseguinolaza G, Pastor MA, Desco M, Fontanellas A. Jericó D, et al. Among authors: lanciego jl. Hum Mol Genet. 2020 Nov 25;29(19):3211-3223. doi: 10.1093/hmg/ddaa204. Hum Mol Genet. 2020. PMID: 32916704
Adeno-associated virus liver transduction efficiency measured by in vivo [18F]FHBG positron emission tomography imaging in rodents and nonhuman primates.
Pañeda A, Collantes M, Beattie SG, Otano I, Snapper J, Timmermans E, Guembe L, Petry H, Lanciego JL, Benito A, Prieto J, Rodriguez-Pena MS, Peñuelas I, Gonzalez-Aseguinolaza G. Pañeda A, et al. Among authors: lanciego jl. Hum Gene Ther. 2011 Aug;22(8):999-1009. doi: 10.1089/hum.2010.190. Epub 2011 Apr 6. Hum Gene Ther. 2011. PMID: 21320035
Glucocerebrosidase Gene Therapy Induces Alpha-Synuclein Clearance and Neuroprotection of Midbrain Dopaminergic Neurons in Mice and Macaques.
Sucunza D, Rico AJ, Roda E, Collantes M, González-Aseguinolaza G, Rodríguez-Pérez AI, Peñuelas I, Vázquez A, Labandeira-García JL, Broccoli V, Lanciego JL. Sucunza D, et al. Among authors: lanciego jl. Int J Mol Sci. 2021 May 1;22(9):4825. doi: 10.3390/ijms22094825. Int J Mol Sci. 2021. PMID: 34062940 Free PMC article.
Recombinant porphobilinogen deaminase targeted to the liver corrects enzymopenia in a mouse model of acute intermittent porphyria.
Córdoba KM, Serrano-Mendioroz I, Jericó D, Merino M, Jiang L, Sampedro A, Alegre M, Corrales F, Garrido MJ, Martini PGV, Lanciego JL, Prieto J, Berraondo P, Fontanellas A. Córdoba KM, et al. Among authors: lanciego jl. Sci Transl Med. 2022 Jan 12;14(627):eabc0700. doi: 10.1126/scitranslmed.abc0700. Epub 2022 Jan 12. Sci Transl Med. 2022. PMID: 35020410
Adeno-Associated Viral Vectors as Versatile Tools for Parkinson's Research, Both for Disease Modeling Purposes and for Therapeutic Uses.
Fajardo-Serrano A, Rico AJ, Roda E, Honrubia A, Arrieta S, Ariznabarreta G, Chocarro J, Lorenzo-Ramos E, Pejenaute A, Vázquez A, Lanciego JL. Fajardo-Serrano A, et al. Among authors: lanciego jl. Int J Mol Sci. 2021 Jun 15;22(12):6389. doi: 10.3390/ijms22126389. Int J Mol Sci. 2021. PMID: 34203739 Free PMC article. Review.
Gene therapy approaches in the non-human primate model of Parkinson's disease.
Pignataro D, Sucunza D, Rico AJ, Dopeso-Reyes IG, Roda E, Rodríguez-Perez AI, Labandeira-Garcia JL, Broccoli V, Kato S, Kobayashi K, Lanciego JL. Pignataro D, et al. Among authors: lanciego jl. J Neural Transm (Vienna). 2018 Mar;125(3):575-589. doi: 10.1007/s00702-017-1681-3. Epub 2017 Jan 27. J Neural Transm (Vienna). 2018. PMID: 28130586 Review.
AAV-PHP.B-Mediated Global-Scale Expression in the Mouse Nervous System Enables GBA1 Gene Therapy for Wide Protection from Synucleinopathy.
Morabito G, Giannelli SG, Ordazzo G, Bido S, Castoldi V, Indrigo M, Cabassi T, Cattaneo S, Luoni M, Cancellieri C, Sessa A, Bacigaluppi M, Taverna S, Leocani L, Lanciego JL, Broccoli V. Morabito G, et al. Among authors: lanciego jl. Mol Ther. 2017 Dec 6;25(12):2727-2742. doi: 10.1016/j.ymthe.2017.08.004. Epub 2017 Aug 10. Mol Ther. 2017. PMID: 28882452 Free PMC article.
135 results