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Multisystem proteinopathy: Where myopathy and motor neuron disease converge.
Muscle Nerve. 2021 Apr;63(4):442-454. doi: 10.1002/mus.27097. Epub 2020 Nov 3.
Muscle Nerve. 2021.
PMID: 33145792
Review.
Development of a standard of care for patients with valosin-containing protein associated multisystem proteinopathy.
Korb M, Peck A, Alfano LN, Berger KI, James MK, Ghoshal N, Healzer E, Henchcliffe C, Khan S, Mammen PPA, Patel S, Pfeffer G, Ralston SH, Roy B, Seeley WW, Swenson A, Mozaffar T, Weihl C, Kimonis V; VCP Standards of Care Working Group.
Korb M, et al.
Orphanet J Rare Dis. 2022 Jan 29;17(1):23. doi: 10.1186/s13023-022-02172-5.
Orphanet J Rare Dis. 2022.
PMID: 35093159
Free PMC article.
Review.
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Provisional practice recommendation for the management of myopathy in VCP-associated multisystem proteinopathy.
Roy B, Peck A, Evangelista T, Pfeffer G, Wang L, Diaz-Manera J, Korb M, Wicklund MP, Milone M, Freimer M, Kushlaf H, Villar-Quiles RN, Stojkovic T, Needham M, Palmio J, Lloyd TE, Keung B, Mozaffar T, Weihl CC, Kimonis V.
Roy B, et al.
Ann Clin Transl Neurol. 2023 May;10(5):686-695. doi: 10.1002/acn3.51760. Epub 2023 Apr 7.
Ann Clin Transl Neurol. 2023.
PMID: 37026610
Free PMC article.
Review.
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Safety and efficacy of zilucoplan in patients with generalised myasthenia gravis (RAISE): a randomised, double-blind, placebo-controlled, phase 3 study.
Howard JF Jr, Bresch S, Genge A, Hewamadduma C, Hinton J, Hussain Y, Juntas-Morales R, Kaminski HJ, Maniaol A, Mantegazza R, Masuda M, Sivakumar K, Śmiłowski M, Utsugisawa K, Vu T, Weiss MD, Zajda M, Boroojerdi B, Brock M, de la Borderie G, Duda PW, Lowcock R, Vanderkelen M, Leite MI; RAISE Study Team.
Howard JF Jr, et al.
Lancet Neurol. 2023 May;22(5):395-406. doi: 10.1016/S1474-4422(23)00080-7.
Lancet Neurol. 2023.
PMID: 37059508
Clinical Trial.
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Design and Statistical Innovations in a Platform Trial for Amyotrophic Lateral Sclerosis.
Quintana M, Saville BR, Vestrucci M, Detry MA, Chibnik L, Shefner J, Berry JD, Chase M, Andrews J, Sherman AV, Yu H, Drake K, Cudkowicz M, Paganoni S, Macklin EA; HEALEY ALS Platform Trial Study Group.
Quintana M, et al.
Ann Neurol. 2023 Sep;94(3):547-560. doi: 10.1002/ana.26714. Epub 2023 Jun 22.
Ann Neurol. 2023.
PMID: 37245090
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Safety and outcomes with efgartigimod use for acetylcholine receptor-positive generalized myasthenia gravis in clinical practice.
Katyal N, Halldorsdottir K, Govindarajan R, Shieh P, Muley S, Reyes P, Leung KK, Mullen J, Milani-Nejad S, Korb M, Goyal NA, Mozaffar T, Goyal N, Habib AA, Muppidi S.
Katyal N, et al.
Muscle Nerve. 2023 Nov;68(5):762-766. doi: 10.1002/mus.27974. Epub 2023 Sep 11.
Muscle Nerve. 2023.
PMID: 37695277
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Crusted scabies triggering autonomic dysreflexia in a patient with spinal cord injury.
Foulad DP, Korb MK, Skupsky H, Smith J.
Foulad DP, et al. Among authors: korb mk.
JAAD Case Rep. 2020 May 19;6(7):640-642. doi: 10.1016/j.jdcr.2020.05.007. eCollection 2020 Jul.
JAAD Case Rep. 2020.
PMID: 32613060
Free PMC article.
No abstract available.
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