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Table representation of search results timeline featuring number of search results per year.
Year | Number of Results |
---|---|
2021 | 5 |
2022 | 3 |
2023 | 1 |
2024 | 0 |
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Page 1
Safety and efficacy of avalglucosidase alfa versus alglucosidase alfa in patients with late-onset Pompe disease (COMET): a phase 3, randomised, multicentre trial.
Lancet Neurol. 2021 Dec;20(12):1012-1026. doi: 10.1016/S1474-4422(21)00241-6.
Lancet Neurol. 2021.
PMID: 34800399
Clinical Trial.
Efficacy and Safety of Avalglucosidase Alfa in Patients With Late-Onset Pompe Disease After 97 Weeks: A Phase 3 Randomized Clinical Trial.
Kishnani PS, Diaz-Manera J, Toscano A, Clemens PR, Ladha S, Berger KI, Kushlaf H, Straub V, Carvalho G, Mozaffar T, Roberts M, Attarian S, Chien YH, Choi YC, Day JW, Erdem-Ozdamar S, Illarioshkin S, Goker-Alpan O, Kostera-Pruszczyk A, van der Ploeg AT, An Haack K, Huynh-Ba O, Tammireddy S, Thibault N, Zhou T, Dimachkie MM, Schoser B; COMET Investigator Group.
Kishnani PS, et al.
JAMA Neurol. 2023 Jun 1;80(6):558-567. doi: 10.1001/jamaneurol.2023.0552.
JAMA Neurol. 2023.
PMID: 37036722
Free PMC article.
Clinical Trial.
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Project "Backtoclinic I": An overview on the state of care of adult PKU patients in Austria.
Beghini M, Resch FJ, Möslinger D, Konstantopoulou V, Karall D, Scholl-Bürgi S, Brunner-Krainz M, Plecko B, Spenger J, Kautzky-Willer A, Scherer T, Hufgard-Leitner M.
Beghini M, et al. Among authors: hufgard leitner m.
Mol Genet Metab. 2021 Jul;133(3):257-260. doi: 10.1016/j.ymgme.2021.05.003. Epub 2021 May 11.
Mol Genet Metab. 2021.
PMID: 34083143
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Sex-Specific Differences in Mortality of Patients with a History of Bariatric Surgery: a Nation-Wide Population-Based Study.
Beiglböck H, Mörth E, Reichardt B, Stamm T, Itariu B, Harreiter J, Hufgard-Leitner M, Fellinger P, Eichelter J, Prager G, Kautzky A, Kautzky-Willer A, Wolf P, Krebs M.
Beiglböck H, et al. Among authors: hufgard leitner m.
Obes Surg. 2022 Jan;32(1):8-17. doi: 10.1007/s11695-021-05763-6. Epub 2021 Nov 9.
Obes Surg. 2022.
PMID: 34751909
Free PMC article.
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Long-term experience with triheptanoin in 12 Austrian patients with long-chain fatty acid oxidation disorders.
Zöggeler T, Stock K, Jörg-Streller M, Spenger J, Konstantopoulou V, Hufgard-Leitner M, Scholl-Bürgi S, Karall D.
Zöggeler T, et al. Among authors: hufgard leitner m.
Orphanet J Rare Dis. 2021 Jan 14;16(1):28. doi: 10.1186/s13023-020-01635-x.
Orphanet J Rare Dis. 2021.
PMID: 33446227
Free PMC article.
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Challenges in Palliative Care Nursing at a University Hospital: A Qualitative Interview Study.
Zeilinger EL, Gabal A, Adamidis F, Popov P, Jaeger K, Hufgard-Leitner M, Brettner R, Titzer H, Masel EK, Unseld M.
Zeilinger EL, et al. Among authors: hufgard leitner m.
J Hosp Palliat Nurs. 2022 Oct 1;24(5):E219-E225. doi: 10.1097/NJH.0000000000000886. Epub 2022 Jun 6.
J Hosp Palliat Nurs. 2022.
PMID: 35666773
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100 years of inherited metabolic disorders in Austria-A national registry of minimal birth prevalence, diagnosis, and clinical outcome of inborn errors of metabolism in Austria between 1921 and 2021.
Ramoser G, Caferri F, Radlinger B, Brunner-Krainz M, Herbst S, Huemer M, Hufgard-Leitner M, Kircher SG, Konstantopoulou V, Löscher W, Möslinger D, Plecko B, Spenger J, Stulnig T, Sunder-Plassmann G, Wortmann S, Scholl-Bürgi S, Karall D; Austrian IMD Registry Group.
Ramoser G, et al. Among authors: hufgard leitner m.
J Inherit Metab Dis. 2022 Mar;45(2):144-156. doi: 10.1002/jimd.12442. Epub 2021 Oct 17.
J Inherit Metab Dis. 2022.
PMID: 34595757
Free PMC article.
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