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Focal lesions following intracerebral gene therapy for mucopolysaccharidosis IIIA.
Ann Clin Transl Neurol. 2023 Jun;10(6):904-917. doi: 10.1002/acn3.51772. Epub 2023 May 11.
Ann Clin Transl Neurol. 2023.
PMID: 37165777
Free PMC article.
Guanabenz ameliorates disease in vanishing white matter mice in contrast to sephin1.
Witkamp D, Oudejans E, Hu-A-Ng GV, Hoogterp L, Krzywańska AM, Žnidaršič M, Marinus K, de Veij Mestdagh CF, Bartelink I, Bugiani M, van der Knaap MS, Abbink TEM.
Witkamp D, et al. Among authors: hu a ng gv.
Ann Clin Transl Neurol. 2022 Aug;9(8):1147-1162. doi: 10.1002/acn3.51611. Epub 2022 Jul 1.
Ann Clin Transl Neurol. 2022.
PMID: 35778832
Free PMC article.
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Pridopidine subtly ameliorates motor skills in a mouse model for vanishing white matter.
Oudejans E, Witkamp D, Hu-A-Ng GV, Hoogterp L, van Rooijen-van Leeuwen G, Kruijff I, Schonewille P, Lalaoui El Mouttalibi Z, Bartelink I, van der Knaap MS, Abbink TE.
Oudejans E, et al. Among authors: hu a ng gv.
Life Sci Alliance. 2024 Jan 3;7(3):e202302199. doi: 10.26508/lsa.202302199. Print 2024 Mar.
Life Sci Alliance. 2024.
PMID: 38171595
Free PMC article.
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Lithium: effects in animal models of vanishing white matter are not promising.
Witkamp D, Oudejans E, Hoogterp L, Hu-A-Ng GV, Glaittli KA, Stevenson TJ, Huijsmans M, Abbink TEM, van der Knaap MS, Bonkowsky JL.
Witkamp D, et al. Among authors: hu a ng gv.
Front Neurosci. 2024 Jan 30;18:1275744. doi: 10.3389/fnins.2024.1275744. eCollection 2024.
Front Neurosci. 2024.
PMID: 38352041
Free PMC article.
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