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Phase I study of liver depot gene therapy in late-onset Pompe disease.
Smith EC, Hopkins S, Case LE, Xu M, Walters C, Dearmey S, Han SO, Spears TG, Chichester JA, Bossen EH, Hornik CP, Cohen JL, Bali D, Kishnani PS, Koeberl DD. Smith EC, et al. Among authors: hornik cp. Mol Ther. 2023 Jul 5;31(7):1994-2004. doi: 10.1016/j.ymthe.2023.02.014. Epub 2023 Feb 18. Mol Ther. 2023. PMID: 36805083 Clinical Trial.
Correction of Biochemical Abnormalities and Improved Muscle Function in a Phase I/II Clinical Trial of Clenbuterol in Pompe Disease.
Koeberl DD, Case LE, Smith EC, Walters C, Han SO, Li Y, Chen W, Hornik CP, Huffman KM, Kraus WE, Thurberg BL, Corcoran DL, Bali D, Bursac N, Kishnani PS. Koeberl DD, et al. Among authors: hornik cp. Mol Ther. 2018 Sep 5;26(9):2304-2314. doi: 10.1016/j.ymthe.2018.06.023. Epub 2018 Jul 5. Mol Ther. 2018. PMID: 30025991 Free PMC article. Clinical Trial.
Use of the complete blood cell count in late-onset neonatal sepsis.
Hornik CP, Benjamin DK, Becker KC, Benjamin DK Jr, Li J, Clark RH, Cohen-Wolkowiez M, Smith PB. Hornik CP, et al. Pediatr Infect Dis J. 2012 Aug;31(8):803-7. doi: 10.1097/INF.0b013e31825691e4. Pediatr Infect Dis J. 2012. PMID: 22531232 Free PMC article.
Fluconazole loading dose pharmacokinetics and safety in infants.
Piper L, Smith PB, Hornik CP, Cheifetz IM, Barrett JS, Moorthy G, Hope WW, Wade KC, Cohen-Wolkowiez M, Benjamin DK Jr. Piper L, et al. Among authors: hornik cp. Pediatr Infect Dis J. 2011 May;30(5):375-8. doi: 10.1097/INF.0b013e318202cbb3. Pediatr Infect Dis J. 2011. PMID: 21085048 Free PMC article.
Comparative efficacy and safety of late surfactant preparations: a retrospective study.
Lane MD, Kishnani S, Udemadu O, Danquah SE, Treadway RM 3rd, Langman A, Balevic S, Jackson WM, Laughon M, Hornik CP, Greenberg RG, Clark RH, Zimmerman KO. Lane MD, et al. Among authors: hornik cp. J Perinatol. 2021 Nov;41(11):2639-2644. doi: 10.1038/s41372-021-01142-2. Epub 2021 Jul 20. J Perinatol. 2021. PMID: 34285358 Free PMC article.
Safety of sildenafil in extremely premature infants: a phase I trial.
Jackson W, Gonzalez D, Smith PB, Ambalavanan N, Atz AM, Sokol GM, Hornik CD, Stewart D, Mundakel G, Poindexter BB, Ahlfeld SK, Mills M, Cohen-Wolkowiez M, Martz K, Hornik CP, Laughon MM; Best Pharmaceuticals for Children Act—Pediatric Trials Network Steering Committee. Jackson W, et al. Among authors: hornik cp, hornik cd. J Perinatol. 2022 Jan;42(1):31-36. doi: 10.1038/s41372-021-01261-w. Epub 2021 Nov 5. J Perinatol. 2022. PMID: 34741102 Free PMC article. Clinical Trial.
235 results