Gray SJ - Search Results

1

Current Clinical Applications of In Vivo Gene Therapy with AAVs.

Mendell JR, Al-Zaidy SA, Rodino-Klapac LR, Goodspeed K, Gray SJ, Kay CN, Boye SL, Boye SE, George LA, Salabarria S, Corti M, Byrne BJ, Tremblay JP. Mendell JR, et al. Among authors: gray sj. Mol Ther. 2021 Feb 3;29(2):464-488. doi: 10.1016/j.ymthe.2020.12.007. Epub 2020 Dec 10. Mol Ther. 2021. PMID: 33309881 Free PMC article. Review.

2

Dystrophin immunity in Duchenne's muscular dystrophy.

Mendell JR, Campbell K, Rodino-Klapac L, Sahenk Z, Shilling C, Lewis S, Bowles D, Gray S, Li C, Galloway G, Malik V, Coley B, Clark KR, Li J, Xiao X, Samulski J, McPhee SW, Samulski RJ, Walker CM. Mendell JR, et al. N Engl J Med. 2010 Oct 7;363(15):1429-37. doi: 10.1056/NEJMoa1000228. N Engl J Med. 2010. PMID: 20925545 Free PMC article. Clinical Trial.

3

Optimizing promoters for recombinant adeno-associated virus-mediated gene expression in the peripheral and central nervous system using self-complementary vectors.

Gray SJ, Foti SB, Schwartz JW, Bachaboina L, Taylor-Blake B, Coleman J, Ehlers MD, Zylka MJ, McCown TJ, Samulski RJ. Gray SJ, et al. Hum Gene Ther. 2011 Sep;22(9):1143-53. doi: 10.1089/hum.2010.245. Epub 2011 Jun 1. Hum Gene Ther. 2011. PMID: 21476867 Free PMC article.

4

Preclinical differences of intravascular AAV9 delivery to neurons and glia: a comparative study of adult mice and nonhuman primates.

Gray SJ, Matagne V, Bachaboina L, Yadav S, Ojeda SR, Samulski RJ. Gray SJ, et al. Mol Ther. 2011 Jun;19(6):1058-69. doi: 10.1038/mt.2011.72. Epub 2011 Apr 12. Mol Ther. 2011. PMID: 21487395 Free PMC article.

5

Phase 1 gene therapy for Duchenne muscular dystrophy using a translational optimized AAV vector.

Bowles DE, McPhee SW, Li C, Gray SJ, Samulski JJ, Camp AS, Li J, Wang B, Monahan PE, Rabinowitz JE, Grieger JC, Govindasamy L, Agbandje-McKenna M, Xiao X, Samulski RJ. Bowles DE, et al. Among authors: gray sj. Mol Ther. 2012 Feb;20(2):443-55. doi: 10.1038/mt.2011.237. Epub 2011 Nov 8. Mol Ther. 2012. PMID: 22068425 Free PMC article. Clinical Trial.

6

Global CNS gene delivery and evasion of anti-AAV-neutralizing antibodies by intrathecal AAV administration in non-human primates.

Gray SJ, Nagabhushan Kalburgi S, McCown TJ, Jude Samulski R. Gray SJ, et al. Gene Ther. 2013 Apr;20(4):450-9. doi: 10.1038/gt.2012.101. Epub 2013 Jan 10. Gene Ther. 2013. PMID: 23303281 Free PMC article.

7

Restoration of cytoskeleton homeostasis after gigaxonin gene transfer for giant axonal neuropathy.

Mussche S, Devreese B, Nagabhushan Kalburgi S, Bachaboina L, Fox JC, Shih HJ, Van Coster R, Samulski RJ, Gray SJ. Mussche S, et al. Among authors: gray sj. Hum Gene Ther. 2013 Feb;24(2):209-19. doi: 10.1089/hum.2012.107. Hum Gene Ther. 2013. PMID: 23316953 Free article.

8

Recent gene therapy advancements for neurological diseases.

Nagabhushan Kalburgi S, Khan NN, Gray SJ. Nagabhushan Kalburgi S, et al. Among authors: gray sj. Discov Med. 2013 Feb;15(81):111-9. Discov Med. 2013. PMID: 23449113 Free PMC article. Review.

9

Clinical applications involving CNS gene transfer.

Kantor B, McCown T, Leone P, Gray SJ. Kantor B, et al. Among authors: gray sj. Adv Genet. 2014;87:71-124. doi: 10.1016/B978-0-12-800149-3.00002-0. Adv Genet. 2014. PMID: 25311921 Free PMC article. Review.

10

Novel Vector Design and Hexosaminidase Variant Enabling Self-Complementary Adeno-Associated Virus for the Treatment of Tay-Sachs Disease.

Karumuthil-Melethil S, Nagabhushan Kalburgi S, Thompson P, Tropak M, Kaytor MD, Keimel JG, Mark BL, Mahuran D, Walia JS, Gray SJ. Karumuthil-Melethil S, et al. Among authors: gray sj. Hum Gene Ther. 2016 Jul;27(7):509-21. doi: 10.1089/hum.2016.013. Hum Gene Ther. 2016. PMID: 27197548 Free PMC article.

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