Goyenvalle A - Search Results

1

Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle.

Morin A, Stantzou A, Petrova ON, Hildyard J, Tensorer T, Matouk M, Petkova MV, Richard I, Manoliu T, Goyenvalle A, Falcone S, Schuelke M, Laplace-Builhé C, Piercy RJ, Garcia L, Amthor H. Morin A, et al. Among authors: goyenvalle a. Proc Natl Acad Sci U S A. 2023 Jan 10;120(2):e2206324120. doi: 10.1073/pnas.2206324120. Epub 2023 Jan 3. Proc Natl Acad Sci U S A. 2023. PMID: 36595689 Free PMC article.

2

Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping.

Goyenvalle A, Vulin A, Fougerousse F, Leturcq F, Kaplan JC, Garcia L, Danos O. Goyenvalle A, et al. Science. 2004 Dec 3;306(5702):1796-9. doi: 10.1126/science.1104297. Epub 2004 Nov 4. Science. 2004. PMID: 15528407

3

[An opening in Duchenne muscular dystrophy: persistent therapeutic rescue of dystrophin by vectorized antisense mediated exon skipping in mdx mice].

Goyenvalle A, Vulin A, Fougerousse F, Leturcq F, Kaplan JC, Garcia L, Danos O. Goyenvalle A, et al. Med Sci (Paris). 2004 Dec;20(12):1163-5. doi: 10.1051/medsci/200420121163. Med Sci (Paris). 2004. PMID: 15581476 Free article. French. No abstract available.

4

Noninvasive monitoring of therapeutic gene transfer in animal models of muscular dystrophies.

Bartoli M, Poupiot J, Goyenvalle A, Perez N, Garcia L, Danos O, Richard I. Bartoli M, et al. Among authors: goyenvalle a. Gene Ther. 2006 Jan;13(1):20-8. doi: 10.1038/sj.gt.3302594. Gene Ther. 2006. PMID: 16107863

5

Gene expression profiling to monitor therapeutic and adverse effects of antisense therapies for Duchenne muscular dystrophy.

't Hoen PA, van der Wees CG, Aartsma-Rus A, Turk R, Goyenvalle A, Danos O, Garcia L, van Ommen GJ, den Dunnen JT, van Deutekom JC. 't Hoen PA, et al. Among authors: goyenvalle a. Pharmacogenomics. 2006 Apr;7(3):281-97. doi: 10.2217/14622416.7.3.281. Pharmacogenomics. 2006. PMID: 16610940

6

Transient immunomodulation allows repeated injections of AAV1 and correction of muscular dystrophy in multiple muscles.

Lorain S, Gross DA, Goyenvalle A, Danos O, Davoust J, Garcia L. Lorain S, et al. Among authors: goyenvalle a. Mol Ther. 2008 Mar;16(3):541-7. doi: 10.1038/sj.mt.6300377. Epub 2008 Jan 8. Mol Ther. 2008. PMID: 18180780 Free article.

7

[Restoration of human dystrophin following transplantation of exon-skipping-engineered DMD patient stem cells into dystrophic mice].

Benchaouir R, Meregalli M, Farini A, D'Antona G, Belicchi M, Goyenvalle A, Battistelli M, Bresolin N, Bottinelli R, Garcia L, Torrente Y. Benchaouir R, et al. Among authors: goyenvalle a. Med Sci (Paris). 2008 Jan;24(1):99-101. doi: 10.1051/medsci/200824199. Med Sci (Paris). 2008. PMID: 18198122 Free article. French. No abstract available.

8

Restoration of human dystrophin following transplantation of exon-skipping-engineered DMD patient stem cells into dystrophic mice.

Benchaouir R, Meregalli M, Farini A, D'Antona G, Belicchi M, Goyenvalle A, Battistelli M, Bresolin N, Bottinelli R, Garcia L, Torrente Y. Benchaouir R, et al. Among authors: goyenvalle a. Cell Stem Cell. 2007 Dec 13;1(6):646-57. doi: 10.1016/j.stem.2007.09.016. Cell Stem Cell. 2007. PMID: 18371406 Free article.

9

Immortalized skin fibroblasts expressing conditional MyoD as a renewable and reliable source of converted human muscle cells to assess therapeutic strategies for muscular dystrophies: validation of an exon-skipping approach to restore dystrophin in Duchenne muscular dystrophy cells.

Chaouch S, Mouly V, Goyenvalle A, Vulin A, Mamchaoui K, Negroni E, Di Santo J, Butler-Browne G, Torrente Y, Garcia L, Furling D. Chaouch S, et al. Among authors: goyenvalle a. Hum Gene Ther. 2009 Jul;20(7):784-90. doi: 10.1089/hum.2008.163. Hum Gene Ther. 2009. PMID: 19358679

10

Enhanced exon-skipping induced by U7 snRNA carrying a splicing silencer sequence: Promising tool for DMD therapy.

Goyenvalle A, Babbs A, van Ommen GJ, Garcia L, Davies KE. Goyenvalle A, et al. Mol Ther. 2009 Jul;17(7):1234-40. doi: 10.1038/mt.2009.113. Epub 2009 May 19. Mol Ther. 2009. PMID: 19455105 Free PMC article.

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