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Current Clinical Applications of In Vivo Gene Therapy with AAVs.
Mendell JR, Al-Zaidy SA, Rodino-Klapac LR, Goodspeed K, Gray SJ, Kay CN, Boye SL, Boye SE, George LA, Salabarria S, Corti M, Byrne BJ, Tremblay JP. Mendell JR, et al. Among authors: goodspeed k. Mol Ther. 2021 Feb 3;29(2):464-488. doi: 10.1016/j.ymthe.2020.12.007. Epub 2020 Dec 10. Mol Ther. 2021. PMID: 33309881 Free PMC article. Review.
The genetics of autism spectrum disorder in an East African familial cohort.
Tuncay IO, DeVries D, Gogate A, Kaur K, Kumar A, Xing C, Goodspeed K, Seyoum-Tesfa L, Chahrour MH. Tuncay IO, et al. Among authors: goodspeed k. Cell Genom. 2023 May 11;3(7):100322. doi: 10.1016/j.xgen.2023.100322. eCollection 2023 Jul 12. Cell Genom. 2023. PMID: 37492102 Free PMC article.
A draft conceptual model of SLC6A1 neurodevelopmental disorder.
Goodspeed K, Mosca LR, Weitzel NC, Horning K, Simon EW, Pfalzer AC, Xia M, Langer K, Freed A, Bone M, Picone M, Bichell TJV. Goodspeed K, et al. Front Neurosci. 2023 Jan 19;16:1026065. doi: 10.3389/fnins.2022.1026065. eCollection 2022. Front Neurosci. 2023. PMID: 36741059 Free PMC article.
Gene Transfer Therapy for Neurodevelopmental Disorders.
Ozlu C, Bailey RM, Sinnett S, Goodspeed KD. Ozlu C, et al. Dev Neurosci. 2021;43(3-4):230-240. doi: 10.1159/000515434. Epub 2021 Apr 21. Dev Neurosci. 2021. PMID: 33882495 Free article. Review.
SLC13A5 Deficiency Disorder: From Genetics to Gene Therapy.
Goodspeed K, Liu JS, Nye KL, Prasad S, Sadhu C, Tavakkoli F, Bilder DA, Minassian BA, Bailey RM. Goodspeed K, et al. Genes (Basel). 2022 Sep 15;13(9):1655. doi: 10.3390/genes13091655. Genes (Basel). 2022. PMID: 36140822 Free PMC article. Review.
Gene Therapy: Novel Approaches to Targeting Monogenic Epilepsies.
Goodspeed K, Bailey RM, Prasad S, Sadhu C, Cardenas JA, Holmay M, Bilder DA, Minassian BA. Goodspeed K, et al. Front Neurol. 2022 Jun 21;13:805007. doi: 10.3389/fneur.2022.805007. eCollection 2022. Front Neurol. 2022. PMID: 35847198 Free PMC article. Review.
Current knowledge of SLC6A1-related neurodevelopmental disorders.
Goodspeed K, Pérez-Palma E, Iqbal S, Cooper D, Scimemi A, Johannesen KM, Stefanski A, Demarest S, Helbig KL, Kang J, Shaffo FC, Prentice B, Brownstein CA, Lim B, Helbig I, De Los Reyes E, McKnight D, Crunelli V, Campbell AJ, Møller RS, Freed A, Lal D. Goodspeed K, et al. Brain Commun. 2020 Oct 13;2(2):fcaa170. doi: 10.1093/braincomms/fcaa170. eCollection 2020. Brain Commun. 2020. PMID: 33241211 Free PMC article. Review.
29 results