Chemical engineering of therapeutic siRNAs for allele-specific gene silencing in Huntington's disease models.
Conroy F, Miller R, Alterman JF, Hassler MR, Echeverria D, Godinho BMDC, Knox EG, Sapp E, Sousa J, Yamada K, Mahmood F, Boudi A, Kegel-Gleason K, DiFiglia M, Aronin N, Khvorova A, Pfister EL.
Conroy F, et al. Among authors: godinho bmdc.
Nat Commun. 2022 Oct 3;13(1):5802. doi: 10.1038/s41467-022-33061-x.
Nat Commun. 2022.
PMID: 36192390
Free PMC article.