Multisystem involvement, defective lysosomes and impaired autophagy in a novel rat model of nephropathic cystinosis.
Krohn P, Rega LR, Harvent M, Festa BP, Taranta A, Luciani A, Dewulf J, Cremonesi A, Camassei FD, Hanson JVM, Gerth-Kahlert C, Emma F, Berquez M, Devuyst O.
Krohn P, et al. Among authors: gerth kahlert c.
Hum Mol Genet. 2022 Jul 7;31(13):2262-2278. doi: 10.1093/hmg/ddac033.
Hum Mol Genet. 2022.
PMID: 35137071
Free PMC article.