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Unlocking loxP to Track Genome Editing In Vivo.
Genes (Basel). 2021 Aug 3;12(8):1204. doi: 10.3390/genes12081204.
Genes (Basel). 2021.
PMID: 34440379
Free PMC article.
Chimeric RNA: DNA TracrRNA Improves Homology-Directed Repair In Vitro and In Vivo.
Simone BW, Lee HB, Daby CL, Ata H, Restrepo-Castillo S, Martínez-Gálvez G, Kar B, Gendron WAC, Clark KJ, Ekker SC.
Simone BW, et al. Among authors: gendron wac.
CRISPR J. 2022 Feb;5(1):40-52. doi: 10.1089/crispr.2021.0087. Epub 2021 Dec 17.
CRISPR J. 2022.
PMID: 34935462
Free PMC article.
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Precision gene editing technology and applications in nephrology.
WareJoncas Z, Campbell JM, Martínez-Gálvez G, Gendron WAC, Barry MA, Harris PC, Sussman CR, Ekker SC.
WareJoncas Z, et al. Among authors: gendron wac.
Nat Rev Nephrol. 2018 Nov;14(11):663-677. doi: 10.1038/s41581-018-0047-x.
Nat Rev Nephrol. 2018.
PMID: 30089813
Free PMC article.
Review.
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Expanding the CRISPR Toolbox with ErCas12a in Zebrafish and Human Cells.
Wierson WA, Simone BW, WareJoncas Z, Mann C, Welker JM, Kar B, Emch MJ, Friedberg I, Gendron WAC, Barry MA, Clark KJ, Dobbs DL, McGrail MA, Ekker SC, Essner JJ.
Wierson WA, et al. Among authors: gendron wac.
CRISPR J. 2019 Dec;2(6):417-433. doi: 10.1089/crispr.2019.0026. Epub 2019 Nov 19.
CRISPR J. 2019.
PMID: 31742435
Free PMC article.
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Suppression-Replacement KCNQ1 Gene Therapy for Type 1 Long QT Syndrome.
Dotzler SM, Kim CSJ, Gendron WAC, Zhou W, Ye D, Bos JM, Tester DJ, Barry MA, Ackerman MJ.
Dotzler SM, et al. Among authors: gendron wac.
Circulation. 2021 Apr 6;143(14):1411-1425. doi: 10.1161/CIRCULATIONAHA.120.051836. Epub 2021 Jan 28.
Circulation. 2021.
PMID: 33504163
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