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Gene expression analysis reveals early dysregulation of disease pathways and links Chmp7 to pathogenesis of spinal and bulbar muscular atrophy.
Sci Rep. 2019 Mar 5;9(1):3539. doi: 10.1038/s41598-019-40118-3.
Sci Rep. 2019.
PMID: 30837566
Free PMC article.
Targeted Molecular Therapies for SBMA.
Rinaldi C, Malik B, Greensmith L.
Rinaldi C, et al.
J Mol Neurosci. 2016 Mar;58(3):335-42. doi: 10.1007/s12031-015-0676-5. Epub 2015 Nov 17.
J Mol Neurosci. 2016.
PMID: 26576772
Review.
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