Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation

Search Page

Filters

My NCBI Filters

Text availability

Article attribute

Article type

Publication date

Search Results

154 results

Filters applied: . Clear all
Results are displayed in a computed author sort order. The Results By Year timeline is not available.
Page 1
Emerging Therapeutic Approaches for Diamond Blackfan Anemia.
Aspesi A, Borsotti C, Follenzi A. Aspesi A, et al. Among authors: follenzi a. Curr Gene Ther. 2018;18(6):327-335. doi: 10.2174/1566523218666181109124538. Curr Gene Ther. 2018. PMID: 30411682 Free PMC article. Review.
Dissecting the transcriptional phenotype of ribosomal protein deficiency: implications for Diamond-Blackfan Anemia.
Aspesi A, Pavesi E, Robotti E, Crescitelli R, Boria I, Avondo F, Moniz H, Da Costa L, Mohandas N, Roncaglia P, Ramenghi U, Ronchi A, Gustincich S, Merlin S, Marengo E, Ellis SR, Follenzi A, Santoro C, Dianzani I. Aspesi A, et al. Among authors: follenzi a. Gene. 2014 Jul 25;545(2):282-9. doi: 10.1016/j.gene.2014.04.077. Epub 2014 May 15. Gene. 2014. PMID: 24835311 Free PMC article.
Lentiviral vector interactions with the host cell.
Borsotti C, Borroni E, Follenzi A. Borsotti C, et al. Among authors: follenzi a. Curr Opin Virol. 2016 Dec;21:102-108. doi: 10.1016/j.coviro.2016.08.016. Epub 2016 Sep 13. Curr Opin Virol. 2016. PMID: 27637073 Review.
Patient-Specific iPSC-Derived Endothelial Cells Provide Long-Term Phenotypic Correction of Hemophilia A.
Olgasi C, Talmon M, Merlin S, Cucci A, Richaud-Patin Y, Ranaldo G, Colangelo D, Di Scipio F, Berta GN, Borsotti C, Valeri F, Faraldi F, Prat M, Messina M, Schinco P, Lombardo A, Raya A, Follenzi A. Olgasi C, et al. Among authors: follenzi a. Stem Cell Reports. 2018 Dec 11;11(6):1391-1406. doi: 10.1016/j.stemcr.2018.10.012. Epub 2018 Nov 8. Stem Cell Reports. 2018. PMID: 30416049 Free PMC article.
Author Correction: Lymphoblastoid cell lines from Diamond Blackfan anaemia patients exhibit a full ribosomal stress phenotype that is rescued by gene therapy.
Aspesi A, Monteleone V, Betti M, Actis C, Morleo G, Sculco M, Guarrera S, Wlodarski MW, Ramenghi U, Santoro C, Ellis SR, Loreni F, Follenzi A, Dianzani I. Aspesi A, et al. Among authors: follenzi a. Sci Rep. 2018 Nov 16;8(1):17227. doi: 10.1038/s41598-018-35522-0. Sci Rep. 2018. PMID: 30442972 Free PMC article.
Flow-Cytometry Platform for Intracellular Detection of FVIII in Blood Cells: A New Tool to Assess Gene Therapy Efficiency for Hemophilia A.
Elnaggar M, Al-Mohannadi A, Kizhakayil D, Raynaud CM, Al-Mannai S, Gentilcore G, Pavlovski I, Sathappan A, Van Panhuys N, Borsotti C, Follenzi A, Grivel JC, Deola S. Elnaggar M, et al. Among authors: follenzi a. Mol Ther Methods Clin Dev. 2019 Nov 15;17:1-12. doi: 10.1016/j.omtm.2019.11.003. eCollection 2020 Jun 12. Mol Ther Methods Clin Dev. 2019. PMID: 31886317 Free PMC article.
Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device.
Olgasi C, Borsotti C, Merlin S, Bergmann T, Bittorf P, Adewoye AB, Wragg N, Patterson K, Calabria A, Benedicenti F, Cucci A, Borchiellini A, Pollio B, Montini E, Mazzuca DM, Zierau M, Stolzing A, Toleikis PM, Braspenning J, Follenzi A. Olgasi C, et al. Among authors: follenzi a. Mol Ther Methods Clin Dev. 2021 Nov 3;23:551-566. doi: 10.1016/j.omtm.2021.10.015. eCollection 2021 Dec 10. Mol Ther Methods Clin Dev. 2021. PMID: 34853801 Free PMC article.
154 results