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In Vitro Investigations on Optimizing and Nebulization of IVT-mRNA Formulations for Potential Pulmonary-Based Alpha-1-Antitrypsin Deficiency Treatment.
Pharmaceutics. 2021 Aug 17;13(8):1281. doi: 10.3390/pharmaceutics13081281.
Pharmaceutics. 2021.
PMID: 34452241
Free PMC article.
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