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Ultrasensitive detection of circulating LINE-1 ORF1p as a specific multi-cancer biomarker.
bioRxiv [Preprint]. 2023 Mar 17:2023.01.25.525462. doi: 10.1101/2023.01.25.525462.
bioRxiv. 2023.
PMID: 36747644
Free PMC article.
Updated.
Preprint.
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy.
Finkel RS, Mercuri E, Darras BT, Connolly AM, Kuntz NL, Kirschner J, Chiriboga CA, Saito K, Servais L, Tizzano E, Topaloglu H, Tulinius M, Montes J, Glanzman AM, Bishop K, Zhong ZJ, Gheuens S, Bennett CF, Schneider E, Farwell W, De Vivo DC; ENDEAR Study Group.
Finkel RS, et al.
N Engl J Med. 2017 Nov 2;377(18):1723-1732. doi: 10.1056/NEJMoa1702752.
N Engl J Med. 2017.
PMID: 29091570
Free article.
Clinical Trial.
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