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Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy: Results of the SMA-TOOL Study.
Neurol Ther. 2023 Feb;12(1):89-105. doi: 10.1007/s40120-022-00411-2. Epub 2022 Oct 21.
Neurol Ther. 2023.
PMID: 36269538
Free PMC article.
Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study).
Madruga-Garrido M, Vázquez-Costa JF, Medina-Cantillo J, Brañas M, Cattinari MG, de Lemus M, Díaz-Abós P, Sánchez-Menéndez V, Terrancle Á, Rebollo P, Maurino J.
Madruga-Garrido M, et al. Among authors: cattinari mg.
Neurol Ther. 2021 Jun;10(1):361-373. doi: 10.1007/s40120-020-00229-w. Epub 2021 Jan 9.
Neurol Ther. 2021.
PMID: 33420962
Free PMC article.
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Treatment of spinal muscular atrophy in European countries: A call to action.
Vázquez-Costa JF, Martínez-Moreno M, Madruga-Garrido M, Munell F, Nascimento A, Pitarch-Castellano I, Pascual-Pascual SI, Povedano M, Cattinari MG.
Vázquez-Costa JF, et al. Among authors: cattinari mg.
Eur J Neurol. 2022 Nov;29(11):3475-3477. doi: 10.1111/ene.15522. Epub 2022 Aug 22.
Eur J Neurol. 2022.
PMID: 35971869
No abstract available.
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Delphi consensus on recommendations for the treatment of spinal muscular atrophy in Spain (RET-AME consensus).
Pitarch Castellano I, Cabrera-Serrano M, Calvo Medina R, Cattinari MG, Espinosa García S, Fernández-Ramos JA, García Campos O, Gómez-Andrés D, Grimalt Calatayud MA, Gutiérrez Martínez AJ, Ibáñez Albert E, Kapetanovic García S, Madruga-Garrido M, Martínez-Moreno M, Medina Cantillo J, Melián Suárez AI, Moreno Escribano A, Munell F, Nascimento Osorio A, Pascual-Pascual SI, Povedano M, Santana Casiano IM, Vázquez-Costa JF.
Pitarch Castellano I, et al. Among authors: cattinari mg.
Neurologia (Engl Ed). 2022 Apr;37(3):216-228. doi: 10.1016/j.nrleng.2021.07.002. Epub 2022 Feb 28.
Neurologia (Engl Ed). 2022.
PMID: 35241415
Free article.
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RegistrAME: the Spanish self-reported patient registry of spinal muscular atrophy.
Cattinari MG, de Lemus M, Tizzano E.
Cattinari MG, et al.
Orphanet J Rare Dis. 2024 Feb 19;19(1):76. doi: 10.1186/s13023-024-03071-7.
Orphanet J Rare Dis. 2024.
PMID: 38373977
Free PMC article.
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Design and Validation of a Clinical Outcome Measure for Adolescents and Adult Patients with Spinal Muscular Atrophy: SMA Life Study Protocol.
Rebollo P, García-López S, Povedano M, Cattinari MG, Martínez-Moreno M, Terrancle Á, Cabello-Moruno R, Vázquez-Costa JF.
Rebollo P, et al. Among authors: cattinari mg.
Neurol Ther. 2024 Feb;13(1):233-249. doi: 10.1007/s40120-023-00571-9. Epub 2024 Jan 5.
Neurol Ther. 2024.
PMID: 38180726
Free PMC article.
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Pain in Children and Adolescents with Spinal Muscular Atrophy: A Longitudinal Study from a Patient Registry.
Pitarch-Castellano I, Hervás D, Cattinari MG, Ibáñez Albert E, López Lobato M, Ñungo Garzón NC, Rojas J, Puig-Ram C, Madruga-Garrido M.
Pitarch-Castellano I, et al. Among authors: cattinari mg.
Children (Basel). 2023 Nov 30;10(12):1880. doi: 10.3390/children10121880.
Children (Basel). 2023.
PMID: 38136082
Free PMC article.
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