Intrauterine enzyme replacement therapies for lysosomal storage disorders: Current developments and promising future prospects.
Herzeg A, Borges B, Lianoglou BR, Gonzalez-Velez J, Canepa E, Munar D, Young SP, Bali D, Gelb MH, Chakraborty P, Kishnani PS, Harmatz P, Cohen JL, MacKenzie TC.
Herzeg A, et al. Among authors: canepa e.
Prenat Diagn. 2023 Dec;43(13):1638-1649. doi: 10.1002/pd.6460. Epub 2023 Nov 13.
Prenat Diagn. 2023.
PMID: 37955580
Review.