Lipid nanoparticles allow efficient and harmless ex vivo gene editing of human hematopoietic cells.
Vavassori V, Ferrari S, Beretta S, Asperti C, Albano L, Annoni A, Gaddoni C, Varesi A, Soldi M, Cuomo A, Bonaldi T, Radrizzani M, Merelli I, Naldini L.
Vavassori V, et al. Among authors: bonaldi t.
Blood. 2023 Aug 31;142(9):812-826. doi: 10.1182/blood.2022019333.
Blood. 2023.
PMID: 37294917
Free PMC article.