Barzel A - Search Results

1

Promoterless Gene Targeting Approach Combined to CRISPR/Cas9 Efficiently Corrects Hemophilia B Phenotype in Neonatal Mice.

Lisjak M, De Caneva A, Marais T, Barbon E, Biferi MG, Porro F, Barzel A, Zentilin L, Kay MA, Mingozzi F, Muro AF. Lisjak M, et al. Among authors: barzel a. Front Genome Ed. 2022 Mar 11;4:785698. doi: 10.3389/fgeed.2022.785698. eCollection 2022. Front Genome Ed. 2022. PMID: 35359664 Free PMC article.

2

Promoterless gene targeting without nucleases rescues lethality of a Crigler-Najjar syndrome mouse model.

Porro F, Bortolussi G, Barzel A, De Caneva A, Iaconcig A, Vodret S, Zentilin L, Kay MA, Muro AF. Porro F, et al. Among authors: barzel a. EMBO Mol Med. 2017 Oct;9(10):1346-1355. doi: 10.15252/emmm.201707601. EMBO Mol Med. 2017. PMID: 28751579 Free PMC article.

3

Coupling AAV-mediated promoterless gene targeting to SaCas9 nuclease to efficiently correct liver metabolic diseases.

De Caneva A, Porro F, Bortolussi G, Sola R, Lisjak M, Barzel A, Giacca M, Kay MA, Vlahoviček K, Zentilin L, Muro AF. De Caneva A, et al. Among authors: barzel a. JCI Insight. 2019 Jun 18;5(15):e128863. doi: 10.1172/jci.insight.128863. JCI Insight. 2019. PMID: 31211694 Free PMC article.

4

Promoterless, Nuclease-Free Genome Editing Confers a Growth Advantage for Corrected Hepatocytes in Mice With Methylmalonic Acidemia.

Chandler RJ, Venturoni LE, Liao J, Hubbard BT, Schneller JL, Hoffmann V, Gordo S, Zang S, Ko CW, Chau N, Chiang K, Kay MA, Barzel A, Venditti CP. Chandler RJ, et al. Among authors: barzel a. Hepatology. 2021 Jun;73(6):2223-2237. doi: 10.1002/hep.31570. Epub 2021 May 21. Hepatology. 2021. PMID: 32976669 Free PMC article.

5

A universal system to select gene-modified hepatocytes in vivo.

Nygaard S, Barzel A, Haft A, Major A, Finegold M, Kay MA, Grompe M. Nygaard S, et al. Among authors: barzel a. Sci Transl Med. 2016 Jun 8;8(342):342ra79. doi: 10.1126/scitranslmed.aad8166. Sci Transl Med. 2016. PMID: 27280686 Free PMC article.

6

Promoterless gene targeting without nucleases ameliorates haemophilia B in mice.

Barzel A, Paulk NK, Shi Y, Huang Y, Chu K, Zhang F, Valdmanis PN, Spector LP, Porteus MH, Gaensler KM, Kay MA. Barzel A, et al. Nature. 2015 Jan 15;517(7534):360-4. doi: 10.1038/nature13864. Epub 2014 Oct 29. Nature. 2015. PMID: 25363772 Free PMC article.

7

Survival Advantage of Both Human Hepatocyte Xenografts and Genome-Edited Hepatocytes for Treatment of α-1 Antitrypsin Deficiency.

Borel F, Tang Q, Gernoux G, Greer C, Wang Z, Barzel A, Kay MA, Shultz LD, Greiner DL, Flotte TR, Brehm MA, Mueller C. Borel F, et al. Among authors: barzel a. Mol Ther. 2017 Nov 1;25(11):2477-2489. doi: 10.1016/j.ymthe.2017.09.020. Epub 2017 Sep 25. Mol Ther. 2017. PMID: 29032169 Free PMC article.

8

Engineered B cells expressing an anti-HIV antibody enable memory retention, isotype switching and clonal expansion.

Nahmad AD, Raviv Y, Horovitz-Fried M, Sofer I, Akriv T, Nataf D, Dotan I, Carmi Y, Burstein D, Wine Y, Benhar I, Barzel A. Nahmad AD, et al. Among authors: barzel a. Nat Commun. 2020 Nov 17;11(1):5851. doi: 10.1038/s41467-020-19649-1. Nat Commun. 2020. PMID: 33203857 Free PMC article.

9

Antibody Repertoire Analysis of Tumor-Infiltrating B Cells Reveals Distinct Signatures and Distributions Across Tissues.

Aizik L, Dror Y, Taussig D, Barzel A, Carmi Y, Wine Y. Aizik L, et al. Among authors: barzel a. Front Immunol. 2021 Jul 19;12:705381. doi: 10.3389/fimmu.2021.705381. eCollection 2021. Front Immunol. 2021. PMID: 34349765 Free PMC article.

10

Frequent aneuploidy in primary human T cells after CRISPR-Cas9 cleavage.

Nahmad AD, Reuveni E, Goldschmidt E, Tenne T, Liberman M, Horovitz-Fried M, Khosravi R, Kobo H, Reinstein E, Madi A, Ben-David U, Barzel A. Nahmad AD, et al. Among authors: barzel a. Nat Biotechnol. 2022 Dec;40(12):1807-1813. doi: 10.1038/s41587-022-01377-0. Epub 2022 Jun 30. Nat Biotechnol. 2022. PMID: 35773341 Free PMC article.

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