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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
2002 8
2003 2
2004 5
2005 4
2006 4
2007 4
2008 8
2009 13
2010 9
2011 13
2012 17
2013 14
2014 10
2015 15
2016 17
2017 13
2018 11
2019 14
2020 8
2021 16
2022 12
2023 16
2024 9

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211 results

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Kenneth I. Berns, MD, PhD [1938-2024].
Byrne BJ, Flotte TR, Herzog RW, Srivastava A. Byrne BJ, et al. Hum Gene Ther. 2024 Mar;35(5-6):133-134. doi: 10.1089/hum.2024.29266.kib. Hum Gene Ther. 2024. PMID: 38497910 No abstract available.
In memoriam: Kenneth I. Berns, MD, PhD (1938-2024).
Byrne BJ, Flotte TR, Herzog RW, Srivastava A. Byrne BJ, et al. Mol Ther. 2024 Apr 3;32(4):867-868. doi: 10.1016/j.ymthe.2024.02.018. Epub 2024 Mar 6. Mol Ther. 2024. PMID: 38452768 No abstract available.
104-week efficacy and safety of cipaglucosidase alfa plus miglustat in adults with late-onset Pompe disease: a phase III open-label extension study (ATB200-07).
Schoser B, Kishnani PS, Bratkovic D, Byrne BJ, Claeys KG, Díaz-Manera J, Laforêt P, Roberts M, Toscano A, van der Ploeg AT, Castelli J, Goldman M, Holdbrook F, Sitaraman Das S, Wasfi Y, Mozaffar T; ATB200-07 Study Group. Schoser B, et al. Among authors: byrne bj. J Neurol. 2024 May;271(5):2810-2823. doi: 10.1007/s00415-024-12236-0. Epub 2024 Feb 28. J Neurol. 2024. PMID: 38418563 Free PMC article. Clinical Trial.
Perspectives of the Friedreich ataxia community on gene therapy clinical trials.
Trantham SJ, Coker MA, Norman S, Crowley E, Berthy J, Byrne BJ, Subramony S, Lou X, Corti M. Trantham SJ, et al. Among authors: byrne bj. Mol Ther Methods Clin Dev. 2023 Dec 18;32(1):101179. doi: 10.1016/j.omtm.2023.101179. eCollection 2024 Mar 14. Mol Ther Methods Clin Dev. 2023. PMID: 38261944 Free PMC article.
The Clinical Development of Taldefgrobep Alfa: An Anti-Myostatin Adnectin for the Treatment of Duchenne Muscular Dystrophy.
Muntoni F, Byrne BJ, McMillan HJ, Ryan MM, Wong BL, Dukart J, Bansal A, Cosson V, Dreghici R, Guridi M, Rabbia M, Staunton H, Tirucherai GS, Yen K, Yuan X, Wagner KR; Taldefgrobep Alfa Study Group. Muntoni F, et al. Among authors: byrne bj. Neurol Ther. 2024 Feb;13(1):183-219. doi: 10.1007/s40120-023-00570-w. Epub 2024 Jan 8. Neurol Ther. 2024. PMID: 38190001 Free PMC article.
Long-term safety and efficacy of cipaglucosidase alfa plus miglustat in individuals living with Pompe disease: an open-label phase I/II study (ATB200-02).
Byrne BJ, Schoser B, Kishnani PS, Bratkovic D, Clemens PR, Goker-Alpan O, Ming X, Roberts M, Vorgerd M, Sivakumar K, van der Ploeg AT, Goldman M, Wright J, Holdbrook F, Jain V, Benjamin ER, Johnson F, Das SS, Wasfi Y, Mozaffar T. Byrne BJ, et al. J Neurol. 2024 Apr;271(4):1787-1801. doi: 10.1007/s00415-023-12096-0. Epub 2023 Dec 6. J Neurol. 2024. PMID: 38057636 Free PMC article. Clinical Trial.
211 results