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Defining genome-wide CRISPR-Cas genome-editing nuclease activity with GUIDE-seq.
Nat Protoc. 2021 Dec;16(12):5592-5615. doi: 10.1038/s41596-021-00626-x. Epub 2021 Nov 12.
Nat Protoc. 2021.
PMID: 34773119
Free PMC article.
Review.
Disease severity impacts plerixafor-mobilized stem cell collection in patients with sickle cell disease.
Leonard A, Sharma A, Uchida N, Stroncek D, Panch SR, West K, Molloy E, Hughes TE, Hauffe S, Taylor T, Fitzhugh C, Hankins JS, Wilson M, Tsai SQ, Weiss MJ, Hsieh M, Tisdale JF.
Leonard A, et al.
Blood Adv. 2021 May 11;5(9):2403-2411. doi: 10.1182/bloodadvances.2021004232.
Blood Adv. 2021.
PMID: 33956057
Free PMC article.
Clinical Trial.
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Chromothripsis as an on-target consequence of CRISPR-Cas9 genome editing.
Leibowitz ML, Papathanasiou S, Doerfler PA, Blaine LJ, Sun L, Yao Y, Zhang CZ, Weiss MJ, Pellman D.
Leibowitz ML, et al.
Nat Genet. 2021 Jun;53(6):895-905. doi: 10.1038/s41588-021-00838-7. Epub 2021 Apr 12.
Nat Genet. 2021.
PMID: 33846636
Free PMC article.
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