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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
2004 1
2005 2
2006 3
2007 2
2008 2
2009 2
2010 2
2011 1
2012 2
2014 1
2015 3
2016 5
2017 5
2018 5
2019 3
2020 8
2021 14
2022 13
2023 9
2024 3

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80 results

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Page 1
Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A.
Ozelo MC, Mahlangu J, Pasi KJ, Giermasz A, Leavitt AD, Laffan M, Symington E, Quon DV, Wang JD, Peerlinck K, Pipe SW, Madan B, Key NS, Pierce GF, O'Mahony B, Kaczmarek R, Henshaw J, Lawal A, Jayaram K, Huang M, Yang X, Wong WY, Kim B; GENEr8-1 Trial Group. Ozelo MC, et al. Among authors: kaczmarek r. N Engl J Med. 2022 Mar 17;386(11):1013-1025. doi: 10.1056/NEJMoa2113708. N Engl J Med. 2022. PMID: 35294811 Clinical Trial.
Hemophilia gene therapy: first, do no harm.
Valentino LA, Kaczmarek R, Pierce GF, Noone D, O'Mahony B, Page D, Rotellini D, Skinner MW. Valentino LA, et al. Among authors: kaczmarek r. J Thromb Haemost. 2023 Sep;21(9):2354-2361. doi: 10.1016/j.jtha.2023.06.016. Epub 2023 Jun 21. J Thromb Haemost. 2023. PMID: 37353081 Free article. Review.
Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A.
Mahlangu J, Kaczmarek R, von Drygalski A, Shapiro S, Chou SC, Ozelo MC, Kenet G, Peyvandi F, Wang M, Madan B, Key NS, Laffan M, Dunn AL, Mason J, Quon DV, Symington E, Leavitt AD, Oldenburg J, Chambost H, Reding MT, Jayaram K, Yu H, Mahajan R, Chavele KM, Reddy DB, Henshaw J, Robinson TM, Wong WY, Pipe SW; GENEr8-1 Trial Group. Mahlangu J, et al. Among authors: kaczmarek r. N Engl J Med. 2023 Feb 23;388(8):694-705. doi: 10.1056/NEJMoa2211075. N Engl J Med. 2023. PMID: 36812433 Clinical Trial.
Treatment-induced hemophilic thrombosis?
Kaczmarek R, Herzog RW. Kaczmarek R, et al. Mol Ther. 2022 Feb 2;30(2):505-506. doi: 10.1016/j.ymthe.2022.01.015. Epub 2022 Jan 20. Mol Ther. 2022. PMID: 35063080 Free PMC article. No abstract available.
Looking to the future of gene therapy for hemophilia A and B.
Kaczmarek R, Herzog RW. Kaczmarek R, et al. Expert Rev Hematol. 2023 Jul-Dec;16(11):807-809. doi: 10.1080/17474086.2023.2268279. Epub 2023 Nov 17. Expert Rev Hematol. 2023. PMID: 37798911 No abstract available.
A Molecular Revolution in the Treatment of Hemophilia.
Butterfield JSS, Hege KM, Herzog RW, Kaczmarek R. Butterfield JSS, et al. Among authors: kaczmarek r. Mol Ther. 2020 Apr 8;28(4):997-1015. doi: 10.1016/j.ymthe.2019.11.006. Epub 2019 Nov 13. Mol Ther. 2020. PMID: 31843450 Free PMC article. Review.
Fusarium Keratitis-Review of Current Treatment Possibilities.
Szaliński M, Zgryźniak A, Rubisz I, Gajdzis M, Kaczmarek R, Przeździecka-Dołyk J. Szaliński M, et al. Among authors: kaczmarek r. J Clin Med. 2021 Nov 23;10(23):5468. doi: 10.3390/jcm10235468. J Clin Med. 2021. PMID: 34884170 Free PMC article. Review.
Eph Receptors and Ephrins in Retinal Diseases.
Kaczmarek R, Gajdzis P, Gajdzis M. Kaczmarek R, et al. Int J Mol Sci. 2021 Jun 8;22(12):6207. doi: 10.3390/ijms22126207. Int J Mol Sci. 2021. PMID: 34201393 Free PMC article. Review.
Factor VIII trafficking to CD4+ T cells shapes its immunogenicity and requires several types of antigen-presenting cells.
Kaczmarek R, Piñeros AR, Patterson PE, Bertolini TB, Perrin GQ, Sherman A, Born J, Arisa S, Arvin MC, Kamocka MM, Martinez MM, Dunn KW, Quinn SM, Morris JJ, Wilhelm AR, Kaisho T, Munoz-Melero M, Biswas M, Kaplan MH, Linnemann AK, George LA, Camire RM, Herzog RW. Kaczmarek R, et al. Blood. 2023 Jul 20;142(3):290-305. doi: 10.1182/blood.2022018937. Blood. 2023. PMID: 37192286 Free PMC article.
80 results