Gene therapy restores the transcriptional program of hematopoietic stem cells in Fanconi anemia.
Lasaga M, Río P, Vilas-Zornoza A, Planell N, Navarro S, Alignani D, Fernández-Varas B, Mouzo D, Zubicaray J, Pujol RM, Nicoletti E, Schwartz JD, Sevilla J, Ainciburi M, Ullate-Agote A, Surrallés J, Perona R, Sastre L, Prosper F, Gomez-Cabrero D, Bueren JA.
Lasaga M, et al. Among authors: fernandez varas b.
Haematologica. 2023 Oct 1;108(10):2652-2663. doi: 10.3324/haematol.2022.282418.
Haematologica. 2023.
PMID: 37021532
Free PMC article.