Safety and efficacy of aceneuramic acid in GNE myopathy: open-label extension study.
Suzuki N, Mori-Yoshimura M, Katsuno M, Takahashi MP, Yamashita S, Oya Y, Hashizume A, Yamada S, Nakamori M, Izumi R, Kato M, Warita H, Tateyama M, Kuroda H, Asada R, Yamaguchi T, Nishino I, Aoki M.
Suzuki N, et al. Among authors: yamaguchi t.
J Neurol Neurosurg Psychiatry. 2024 Jun 5:jnnp-2024-333853. doi: 10.1136/jnnp-2024-333853. Online ahead of print.
J Neurol Neurosurg Psychiatry. 2024.
PMID: 38839274
Free article.
No abstract available.