Fitusiran prophylaxis in people with hemophilia A or B who switched from prior BPA/CFC prophylaxis: the ATLAS-PPX trial.
Kenet G, Nolan B, Zulfikar B, Antmen B, Kampmann P, Matsushita T, You CW, Vilchevska K, Bagot CN, Sharif A, Peyvandi F, Young G, Negrier C, Chi J, Kittner B, Sussebach C, Shammas F, Mei B, Andersson S, Kavakli K.
Kenet G, et al. Among authors: kavakli k.
Blood. 2024 May 30;143(22):2256-2269. doi: 10.1182/blood.2023021864.
Blood. 2024.
PMID: 38452197
Free article.
Clinical Trial.