MiR34 contributes to spinal muscular atrophy and AAV9-mediated delivery of MiR34a ameliorates the motor deficits in SMA mice.
Chen TH, Chang SH, Wu YF, Yen YP, Hsu FY, Chen YC, Ming Y, Hsu HC, Su YC, Wong ST, Hung JH, Chiou SH, Jong YJ, Chen JA.
Chen TH, et al. Among authors: chen ja, chen yc.
Mol Ther Nucleic Acids. 2023 Mar 15;32:144-160. doi: 10.1016/j.omtn.2023.03.005. eCollection 2023 Jun 13.
Mol Ther Nucleic Acids. 2023.
PMID: 37064776
Free PMC article.